Al Rayyan
Al Rayyan
Al Rayyan, Qatar2 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Recruiting | Phase 4 | 2026-09-10 | NCT05861999 | |
| RZ358 Treatment for Congenital Hyperinsulinism | Congenital Hyperinsulinism, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, glucose metabolism disease, hyperinsulinism, hypoglycemia, metabolic disease, pancreas disorder | Active, not recruiting | Phase 3 | 2026-01-08 | NCT06208215 |