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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or ThalassaemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemiaRecruitingPhase 32026-09-18NCT06609226
A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle Eastβ-thalassemiaRecruitingNot stated2026-08-19NCT07215975
A Study of Etavopivat in Adults and Adolescents With Sickle Cell Disease (HIBISCUS)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sickle Cell Trait, Vaso-Occlusive Crises, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseActive, not recruitingPhase 32026-04-06NCT04624659
AutoInflammatory Disease Alliance Registry (AIDA)Behcet disease, Castleman disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Marshall syndrome, PFAPA syndrome, Schnitzler syndrome, Skin and Connective Tissue Diseases, Spondylarthritis, Stomatognathic Diseases, VEXAS syndrome, anterior uveitis, arthritic joint disease, arthropathy, autoimmune disease, bone disorder, cardiovascular disorder, connective tissue disorder, eye disorder, hereditary disease, hereditary periodic fever syndrome, hereditary skin disorder, immune system disorder, immunoproliferative disorder, juvenile idiopathic arthritis, lymphatic system disorder, lymphoproliferative syndrome, monoclonal gammopathy, monoclonal gammopathy of uncertain significance, mouth disorder, musculoskeletal system disorder, panuveitis, rheumatic disorder, scleral disorder, scleritis, skin disorder, skin vascular disease, spondylitis, systemic-onset juvenile idiopathic arthritis, uveal disorder, uveitis, vascular disorder, vasculitis, vertebral column disorderRecruitingNot stated2025-07-10NCT05200715
Assessment of Gastrointestinal Discomfort and Infections in Healthy Term InfantsInfectionsActive, not recruitingNot stated2024-12-20NCT06744699