14 results · Page 1 of 1

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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of KarXT + KarX-EC for Treatment of Irritability in Children and Adolescents With Autism Spectrum Disorderautism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderNot yet recruitingPhase 32026-09-28NCT07285798
A Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid SyndromePhelan-McDermid syndromeRecruitingPhase 32026-09-28NCT07281079
Registry for Participants With Short Bowel SyndromeDigestive System Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, digestive system disorder, intestinal disorder, malabsorption syndrome, short bowel syndromeActive, not recruitingNot stated2026-09-23NCT01990040
A Study to Evaluate the Long-term Safety and Tolerability of Xanomeline and Trospium Chloride for the Treatment of Psychiatric Disorders in Children and AdolescentsSchizophrenia Spectrum and Other Psychotic Disorders, autism, autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorder, schizophreniaRecruitingPhase 32026-09-22NCT07424404
An Open-label Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid SyndromePhelan-McDermid syndromeRecruitingPhase 32026-09-21NCT07593391
Buspirone for Anxiety in Autistic Youthanxiety, anxiety disorder, autism, autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderRecruitingPhase 42026-09-17NCT07439042
Gaucher Disease Outcome Survey (GOS)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisRecruitingNot stated2026-09-15NCT03291223
A Natural History Study of Angelman SyndromeAbnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderRecruitingNot stated2026-08-21NCT07417137
Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)Abnormalities, Multiple, Arrhythmias, Cardiac, COVID-19, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronaviridae Infections, Down syndrome, Dyssomnias, Edema, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Hemic and Lymphatic Diseases, Hemorrhage, Infant, Newborn, Diseases, Infant, Premature, Diseases, Infections, Inflammation, Kawasaki disease, Lung Injury, Menorrhagia, Menstruation Disturbances, Neurobehavioral Manifestations, Neurologic Manifestations, Nidovirales infectious disease, Nutritional and Metabolic Diseases, Orthocoronavirinae infectious disease, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, Signs and Symptoms, Skin and Connective Tissue Diseases, Sleep Disorders, Intrinsic, Suppuration, Urogenital Diseases, Uterine Hemorrhage, Ventilator-Induced Lung Injury, Water-Electrolyte Imbalance, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, attention deficit hyperactivity disorder, inattentive type, blood coagulation disease, bronchopulmonary dysplasia, cardiovascular disorder, cellulitis, chromosomal disorder, coagulation protein disease, connective tissue disorder, endocrine system disorder, female reproductive system disorder, heart disorder, heart failure, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, hyperaldosteronism, hyperphosphatemia, hypertensive disorder, inherited blood coagulation disorder, insomnia, intellectual disability, lung disorder, lymphatic system disorder, metabolic disease, nervous system disorder, neurodevelopmental disorder, oppositional defiant disorder, pediatric multisystem inflammatory disease, COVID-19 related, phosphorus metabolism disease, pneumonia, potassium deficiency disease, primary aldosteronism, psychiatric disorder, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, respiratory tract infectious disorder, skin disorder, skin disorder caused by infection, skin infection, skin vascular disease, sleep-wake disorder, uterine disorder, vascular disorder, vascular hemostatic disease, vasculitis, viral infectious disease, viral pneumoniaRecruitingNot stated2026-08-21NCT04278404
Prednisone in Adults With an Immune-Mediated Subtype of Autism Spectrum DisorderInflammation, Neuroinflammatory Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, autism, autism spectrum disorder, autoimmune disease, immune system disorder, nervous system disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderRecruitingEarly phase 12026-08-19NCT06934915
A Study Evaluating the Efficacy and Safety of Adjuvant Giredestrant Compared With Physician's Choice of Adjuvant Endocrine Monotherapy in Participants With Estrogen Receptor-Positive, HER2-Negative Early Breast Cancer (lidERA Breast Cancer)Neoplasms by Site, Skin and Connective Tissue Diseases, breast disorder, breast neoplasm, neoplasm, skin disorderActive, not recruitingPhase 32026-06-17NCT04961996
Direct to Patient Minimal Risk Biospecimen and Data Collection ResearchBronchiolitis Obliterans, Digestive System Diseases, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, celiac disease, cryptogenic organizing pneumonia, digestive system disorder, graft versus host disease, immune system disorder, intestinal disorder, kidney disorder, lung disorder, malabsorption syndrome, metabolic disease, obstructive lung disease, respiratory system disorder, urinary system disorderRecruitingNot stated2026-05-05NCT07128966
Leucovorin for the Treatment of Language Impairment in Children With Autism Spectrum DisorderNeurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, autism spectrum disorder, communication disorder, language disorder, nervous system disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderActive, not recruitingPhase 22026-04-27NCT02839915
Collection and Distribution of Biospecimens for Novel Research UsesDisease Attributes, Hemic and Lymphatic Diseases, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, autoimmune disease, cancer, hematologic disorder, immune system disorder, infectious disease, neoplasm, skin disorderRecruitingNot stated2022-11-09NCT03848962