Gordonville
Gordonville
Gordonville, Pennsylvania, United States2 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of MZE782 in Adults With PKU | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Recruiting | Phase 2 | 2026-10-08 | NCT07694440 | |
| WiTNNess - TNNT1 Myopathy Natural History Study | congenital structural myopathy, hereditary skeletal muscle disorder, muscle tissue disorder, musculoskeletal system disorder, nemaline myopathy, nemaline myopathy 5, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-06-23 | NCT06374719 |