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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety, Tolerability, and Pharmacokinetics of SVG103 (Paxalisib) in Focal Cortical Dysplasia Type II (FCD-II), Tuberous Sclerosis Complex (TSC) or Hemimegalencephaly (HME)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Focal Cortical Dysplasia, Malformations of Cortical Development, Group I, Musculoskeletal Abnormalities, Neoplasms, Multiple Primary, central nervous system malformation, cerebral cortical dysplasia, hamartoma, hemimegalencephaly, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, megalencephaly, musculoskeletal system disorder, neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, tuberous sclerosisRecruitingPhase 1 / Phase 22026-08-10NCT07287202
Fluorescence Guided Focal Cortical Dysplasia SurgeryCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Drug Resistant Epilepsy, Focal Cortical Dysplasia, Malformations of Cortical Development, Group I, brain disorder, central nervous system disorder, central nervous system malformation, cerebral cortical dysplasia, epilepsy, nervous system disorderNot yet recruitingPhase 22026-06-18NCT07657975
Genetic and Electrophysiologic Study in Focal Drug-resistant EpilepsiesCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Focal Cortical Dysplasia, Malformations of Cortical Development, Group I, Musculoskeletal Abnormalities, Neoplasms, Multiple Primary, Neuroinflammatory Diseases, brain disorder, central nervous system disorder, central nervous system malformation, cerebral cortical dysplasia, congenital hypothalamic hamartoma syndrome, encephalitis, epilepsy, focal epilepsy, hamartoma, hemimegalencephaly, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, megalencephaly, musculoskeletal system disorder, neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, tuberous sclerosisRecruitingNot stated2026-04-17NCT02890641
Astroscape: A Study of Radiprodil on Safety, Tolerability, Pharmacokinetics, and Effect on Seizures and Behavioral Symptoms in Patients With TSC or FCD Type IICongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Focal Cortical Dysplasia, Malformations of Cortical Development, Group I, Neoplasms, Multiple Primary, central nervous system malformation, cerebral cortical dysplasia, hamartoma, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, tuberous sclerosisActive, not recruitingPhase 1 / Phase 22026-04-01NCT06392009
Mos-FED (Mosaicism in Focal Epilepsy Cortical Dysplasia Tissue)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Focal Cortical Dysplasia, Malformations of Cortical Development, Group I, brain disorder, central nervous system disorder, central nervous system malformation, cerebral cortical dysplasia, epilepsy, nervous system disorderRecruitingNot applicable2024-10-23NCT06053671