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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess the Tolerability of Ianalumab (VAY736) With Investigator's Choice Thrombopoietin Receptor Agonist (IC TPO-RA) in Patients With Primary Immune Thrombocytopenia (ITP)Cytopenia, Evans syndrome, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingPhase 22026-10-09NCT07421167
A Study of Pirtobrutinib in Participants With Immune ThrombocytopeniaCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingPhase 1 / Phase 22026-10-09NCT06721013
Haploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 DepletionBone Marrow Failure Disorders, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Disease Attributes, Hemic and Lymphatic Diseases, Leukemia, Myelogenous, Chronic, BCR-ABL Positive, Lymphohistiocytosis, Hemophagocytic, Myeloproliferative Disorders, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Primary Immunodeficiency Diseases, acute myeloid leukemia, anemia, aplastic anemia, bone marrow disorder, hematologic disorder, hereditary disease, histiocytosis, immune system disorder, immunoproliferative disorder, inborn error of immunity, inherited hemoglobinopathy, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, myelodysplastic syndrome, myeloid leukemia, neoplasm, non-Langerhans cell histiocytosisActive, not recruitingNot applicable2026-10-08NCT05236764
Etiology, Pathogenesis, and Natural History of Idiopathic CD4+ LymphocytopeniaBacterial Infections and Mycoses, Central Nervous System Fungal Infections, Cryptococcal meningitis, Cytopenia, DNA Virus Infections, Hemic and Lymphatic Diseases, Infections, Neuroinflammatory Diseases, Opportunistic Infections, Skin Diseases, Viral, Skin and Connective Tissue Diseases, Tumor Virus Infections, autoimmune disease, central nervous system disorder, central nervous system infectious disorder, common wart, cryptococcosis, fungal infectious disease, fungal meningitis, hematologic disorder, human papilloma virus infection, idiopathic CD4-positive T-lymphocytopenia, immune system disorder, inborn error of immunity, leukocyte disorder, leukopenia, lymphopenia, meningitis, nervous system disorder, skin disorder, skin disorder caused by infection, viral infectious diseaseRecruitingNot stated2026-10-08NCT00867269
Screening for Hematology Branch ProtocolsCytopenia, Hemic and Lymphatic Diseases, Neoplasms by Site, Pathologic Processes, Pathological Conditions, Signs and Symptoms, agranulocytosis, anemia, blood platelet disease, disease, hematologic disorder, hematopoietic and lymphoid system neoplasm, leukocyte disorder, leukopenia, neoplasm, neutropenia, thrombocytopeniaEnrolling by invitationNot stated2026-10-08NCT00001620
A Study in Children and, Adults With Congenital Thrombotic Thrombocytopenic Purpura (cTTP) Treated With AdzynmaCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, blood coagulation disease, blood platelet disease, hematologic disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombophilia, thrombotic microangiopathy, thrombotic thrombocytopenic purpuraRecruitingNot stated2026-10-02NCT07353099
A Study of Patients' Preferences for Primary Immune Thrombocytopenia TreatmentCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingNot stated2026-10-01NCT07786077
A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS)Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingPhase 32026-10-01NCT04958265
Comparative Autoantibody and Immunologic Cell Marker StudyAIDS, Blood-Borne Infections, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, DNA Virus Infections, Digestive System Diseases, Disease Attributes, Epstein-Barr virus infection, Flaviviridae infectious disease, Genital Diseases, Guillain-Barre syndrome, HIV infectious disease, Hemic and Lymphatic Diseases, Hemorrhage, Herpesviridae infectious disease, Immunoglobulin G4-Related Disease, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Post-Infectious Disorders, Purpura, Thrombocytopenic, Idiopathic, RNA Virus Infections, Sepsis, Signs and Symptoms, Sjogren syndrome, Skin Manifestations, Skin and Connective Tissue Diseases, Slow Virus Diseases, Stomatognathic Diseases, Systemic Inflammatory Response Syndrome, Tumor Virus Infections, Undifferentiated Connective Tissue Diseases, Urogenital Diseases, Xerostomia, arthritic joint disease, arthropathy, autoimmune disease, autoimmune disorder of the nervous system, autoimmune lymphoproliferative syndrome, blood coagulation disease, blood platelet disease, connective tissue disorder, demyelinating disease, diffuse scleroderma, dry eye syndrome, eye disorder, graft versus host disease, hematologic disorder, hemorrhagic disease, hepatitis, hepatitis C virus infection, hereditary disease, immune system disorder, immunoproliferative disorder, inborn error of immunity, infectious disease, juvenile idiopathic arthritis, lacrimal apparatus disorder, lentivirus infection, liver disorder, lymphatic system disorder, lymphoproliferative syndrome, mouth disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, polyradiculoneuropathy, purpura, rheumatic disorder, rheumatoid arthritis, salivary gland disorder, sexually transmitted disease, skin disorder, systemic lupus erythematosus, systemic sclerosis, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathy, uterine carcinosarcoma, viral hepatitis, viral infectious disease, viral sexually transmitted diseaseEnrolling by invitationNot stated2026-10-01NCT02422875
TGD001 Treatment in Thrombotic MicroangiopathiesCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyNot yet recruitingPhase 1 / Phase 22026-09-29NCT07459114
the Efficacy of Leucogen in Preventing the Risk of Ribociclib-Associated Neutropenia in Early Breast CancerCytopenia, Hemic and Lymphatic Diseases, Neoplasms by Site, Skin and Connective Tissue Diseases, agranulocytosis, breast cancer, breast disorder, breast neoplasm, hematologic disorder, leukocyte disorder, leukopenia, neoplasm, neutropenia, skin disorderRecruitingPhase 22026-09-28NCT07380646
CHIP/CCUS Natural History ProtocolCytopenia, Hemic and Lymphatic Diseases, bone marrow disorder, clonal hematopoiesis of indeterminate potential, hematologic disorder, myelodysplastic syndromeRecruitingNot stated2026-09-28NCT04102423
Safety of Belimumab in People With Idiopathic CD4 Lymphopenia and Autoantibodies (Phoebe)Cytopenia, Hemic and Lymphatic Diseases, autoimmune disease, hematologic disorder, idiopathic CD4-positive T-lymphocytopenia, immune system disorder, inborn error of immunity, leukocyte disorder, leukopenia, lymphopeniaRecruitingPhase 12026-09-28NCT04097561
Restrictive Versus Standard Antibiotic Treatment During CAR-T TherapyBlood Protein Disorders, Cytopenia, Febrile Neutropenia, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, agranulocytosis, cardiovascular disorder, hematologic disorder, hemorrhagic disease, immune system disorder, immunoproliferative disorder, leukocyte disorder, leukopenia, lymphoproliferative syndrome, monoclonal gammopathy, neoplasm, neutropenia, plasma cell neoplasm, vascular disorder, vascular hemostatic diseaseNot yet recruitingPhase 22026-09-25NCT07842198
A Study of Nipocalimab or Intravenous Immunoglobulin (IVIG) in Pregnancies At Risk of Fetal and Neonatal Alloimmune Thrombocytopenia (FNAIT)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, blood platelet disease, hematologic disorder, neonatal thrombocytopenia, thrombocytopeniaRecruitingPhase 32026-09-25NCT06533098
A Study of Nipocalimab in Reducing the Risk of Fetal and Neonatal Alloimmune Thrombocytopenia (FNAIT)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, blood platelet disease, hematologic disorder, neonatal thrombocytopenia, thrombocytopeniaRecruitingPhase 32026-09-25NCT06449651
Antibiotic Duration and Outcomes in High-Risk Febrile Neutropenia PatientsCytopenia, Febrile Neutropenia, Hemic and Lymphatic Diseases, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Systemic Inflammatory Response Syndrome, agranulocytosis, hematologic disorder, leukocyte disorder, leukopenia, neutropeniaRecruitingNot applicable2026-09-24NCT07372131
A Study of Efgartigimod IV in Participants From 12 Years to Less Than 18 Years of Age With Chronic Immune Thrombocytopenia (ITP)Cytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, autoimmune thrombocytopenic purpura, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingPhase 2 / Phase 32026-09-24NCT07194850
A Study of Ianalumab (VAY736) in Patients With Primary Immune Thrombocytopenia (ITP) Previously Treated With at Least Two Lines of TherapiesCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyActive, not recruitingPhase 22026-09-24NCT05885555
Phase 1 Dose Escalation Study of RXIM002 in Autoimmune CytopeniasCytopenia, Disease Attributes, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Recurrence, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyNot yet recruitingPhase 12026-09-23NCT07765966
A Phase 3 Study to Evaluate the Safety and Efficacy of Efgartigimod PH20 Subcutaneous in Adult Patients With Primary Immune ThrombocytopeniaCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyActive, not recruitingPhase 32026-09-23NCT04812925
Safety and Preliminary Efficacy of CTX112 in Adult Participants With Relapsed/Refractory Hematologic Autoimmune DiseaseCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, autoimmune hemolytic anemia, warm type, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingPhase 1 / Phase 22026-09-22NCT07549698
Collection of Human Samples to Study Hairy Cell and Other Leukemias, and to Develop Recombinant Immunotoxins for Cancer TreatmentB-cell chronic lymphocytic leukemia, Chronic Disease, Cytopenia, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Leukemia, B-Cell, Male Urogenital Diseases, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Precursor T-Cell Lymphoblastic Leukemia-Lymphoma, T-cell non-Hodgkin lymphoma, Urogenital Diseases, anemia, blood platelet disease, hairy cell leukemia, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, immune system disorder, immunoproliferative disorder, kidney disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, primary cutaneous T-cell non-Hodgkin lymphoma, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2026-09-22NCT01087333
Efficacy and Safety of Romiplostim N01 for Injection in Promoting Platelet Reconstitution After Allogeneic Hematopoietic Stem Cell TransplantationCytopenia, Hemic and Lymphatic Diseases, blood platelet disease, hematologic disorder, thrombocytopeniaNot yet recruitingPhase 22026-09-21NCT07829952
Study of Trilaciclib and LurbinectidinCytopenia, Hemic and Lymphatic Diseases, Neoplasms by Site, Thoracic Neoplasms, agranulocytosis, bronchial neoplasm, bronchogenic carcinoma, hematologic disorder, leukocyte disorder, leukopenia, lung cancer, lung disorder, lung neoplasm, neoplasm, neutropenia, respiratory system disorder, respiratory tract neoplasm, small cell lung carcinomaRecruitingPhase 22026-09-21NCT05578326