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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
GMEB-SASS: A Gene-Modified Skin Substitute for RDEB TreatmentCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 1 / Phase 22026-03-18NCT07193134
Ex Vivo Gene Therapy Clinical Trial for RDEB Using Genetically Corrected Autologous Skin Equivalent GraftsCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 1 / Phase 22026-02-12NCT04186650
A Natural History Study of Corneal Abrasions in Patients With Dystrophic Epidermolysis Bullosa (DEB)Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, nervous system disorder, nervous system injury, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2025-07-02NCT06563414