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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase 2/3 Clinical Study of QRX003 Lotion in Subjects With Netherton SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingPhase 2 / Phase 32026-09-28NCT07538583
Clinical Study of QRX003 Lotion in Subjects With Netherton SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingPhase 2 / Phase 32026-08-31NCT06953466
Open Label, Safety and Efficacy Study of QRX003 Lotion in Subjects With Netherton SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingPhase 2 / Phase 32026-08-31NCT05789056
A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingPhase 12026-08-27NCT06539507
Epidermal Growth Factor Receptor Inhibition for KeratinopathiesAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Keratoderma, Palmoplantar, Skin Abnormalities, Skin and Connective Tissue Diseases, ectodermal dysplasia syndrome, epidermolytic ichthyosis, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, nail disorder, pachyonychia congenita, skin disorderNot yet recruitingPhase 1 / Phase 22026-08-03NCT06545695
Study of Skin and Gut Microbiome in a Skin Condition Involving Skin Barrier Impairment and Allergic Symptoms: Netherton SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingNot stated2026-06-30NCT07280091
Defining the Skin and Blood Biomarkers of IchthyosisAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderEnrolling by invitationNot stated2026-04-27NCT03417856
Lymphocyte Phenotype of Autosomal Recessive Congenital Ichthyoses Mutated NIPAL4 (Nipal4-nEDD)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Neoplasms by Histologic Type, Sezary syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, T-cell non-Hodgkin lymphoma, autosomal recessive congenital ichthyosis 1, hereditary disease, hereditary skin disorder, ichthyosis, immune system disorder, immunoproliferative disorder, keratosis, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, primary cutaneous T-cell non-Hodgkin lymphoma, skin disorderNot yet recruitingNot stated2026-03-17NCT07477769
Safety, Tolerability and Efficacy of QRX003 Lotion in Subjects With Netherton SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderActive, not recruitingPhase 2 / Phase 32026-03-16NCT05521438