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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Growth Evaluation, Health Promotion, and Clinical Management in Children and Adolescents With ThalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Puberty, Delayed, Thalassemia Intermedia, Thalassemia Major, anemia, beta thalassemia, endocrine system disorder, familial hemolytic anemia, gonadal disorder, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingNot applicable2026-09-18NCT06931912
Risk Factors Affecting Growth in Thalassemic Children at AUCHCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaNot yet recruitingNot stated2026-04-03NCT07509996
Gonadal Function in Thalassemic PatientCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaNot yet recruitingNot stated2025-12-17NCT07288762
Effect of Incentive Respiratory Training on Pulmonary Functions and Functional Capacity in Children With B-thalassemia MajorCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingNot applicable2025-08-08NCT07112703
Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta ThalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingPhase 22025-05-30NCT06490627
The Effect of Laughter Yoga in Beta Thalassaemia Major Patients: a Randomised Controlled TrialCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyssomnias, Fatigue, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Sleep Disorders, Intrinsic, Thalassemia Major, anemia, beta thalassemia, beta-thalassemia major, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, insomnia, nervous system disorder, psychiatric disorder, sleep-wake disorder, thalassemiaNot yet recruitingNot applicable2025-05-20NCT06980662
Study to Evaluate the Long- Term Safety and Efficacy of Luspatercept in Subjects Who Received at Least One Dose of Luspatercept in the Compassionate Use PhaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingNot stated2025-04-06NCT06913634
EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Intermedia, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingPhase 1 / Phase 22025-04-02NCT05444894
To Evaluate Long- Term Safety and Efficacy of LuspaterceptCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingNot stated2025-03-13NCT06875219
Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingNot applicable2024-12-16NCT06734520