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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Prescreening Study to Identify Potential Stargardt Participants for ACDN-01 Clinical Trials (STARPATH)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Juvenile Macular Degeneration, Stargardt Disease 1, Stargardt disease, cone-rod dystrophy, eye disorder, hereditary disease, inherited retinal dystrophy, macular degeneration, retinal degeneration, retinal disorderRecruitingNot stated2026-10-09NCT06445322
Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Juvenile Macular Degeneration, Stargardt Disease 1, Stargardt disease, cone-rod dystrophy, eye disorder, hereditary disease, inherited retinal dystrophy, macular degeneration, retinal degeneration, retinal disorderRecruitingPhase 1 / Phase 22026-10-07NCT06467344
A Phase 1, First-in-Human Study of CITY-RBP4 in Healthy Volunteers and STGD1 ParticipantsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt Disease 1, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderRecruitingPhase 12026-09-23NCT07836452
Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt Disease 1, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderRecruitingPhase 1 / Phase 22026-09-02NCT07002398
A Phase 2/3 Study to Evaluate the Efficacy and Safety of Tinlarebant in Subjects With Stargardt DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt Disease 1, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderActive, not recruitingPhase 2 / Phase 32026-03-12NCT06388083
Function and Imaging Assessments for G1961E-associated Stargardt DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt Disease 1, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderActive, not recruitingNot stated2025-04-22NCT05674058
Safety and Efficacy of a Single Subretinal Injection of JWK006 Gene Therapy in Subjects With Stargardt Disease(STGD1)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt Disease 1, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderActive, not recruitingPhase 1 / Phase 22024-03-08NCT06300476