hereditary hyperbilirubinemia
hereditary hyperbilirubinemia
Explore linked clinical trials. Standard reference: MONDO:00024085 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Therapy for Crigler Najjar Syndrome Type I (AlphaCN) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic disease | Recruiting | Phase 1 / Phase 2 | 2025-01-13 | NCT06641154 | |
| Spanish Registry of Autoimmune and Cholestatic Liver Diseases (ColHai) | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Cholangitis, Sclerosing, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, Dubin-Johnson syndrome, Fibrosis, Hyperbilirubinemia, Neonatal, Infant, Newborn, Diseases, Jaundice, Neonatal, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholangitis, cholestasis, cirrhosis of liver, congenital heart disease, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, intrahepatic cholestasis, liver disorder, metabolic disease, primary biliary cholangitis | Recruiting | Not stated | 2025-01-10 | NCT06767605 | |
| Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic disease | Recruiting | Phase 2 | 2024-12-03 | NCT06518005 | |
| Gene Therapy for Severe Crigler Najjar Syndrome | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic disease | Recruiting | Not applicable | 2023-03-28 | NCT03466463 | |
| China Registry for Genetic / Metabolic Liver Diseases | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, iron metabolism disease, iron poisoning, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative disease | Recruiting | Not stated | 2017-04-27 | NCT03131427 |