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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy for Crigler Najjar Syndrome Type I (AlphaCN)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 1 / Phase 22025-01-13NCT06641154
Spanish Registry of Autoimmune and Cholestatic Liver Diseases (ColHai)Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Cholangitis, Sclerosing, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, Dubin-Johnson syndrome, Fibrosis, Hyperbilirubinemia, Neonatal, Infant, Newborn, Diseases, Jaundice, Neonatal, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholangitis, cholestasis, cirrhosis of liver, congenital heart disease, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, intrahepatic cholestasis, liver disorder, metabolic disease, primary biliary cholangitisRecruitingNot stated2025-01-10NCT06767605
Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 22024-12-03NCT06518005
Gene Therapy for Severe Crigler Najjar SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingNot applicable2023-03-28NCT03466463
China Registry for Genetic / Metabolic Liver DiseasesBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, iron metabolism disease, iron poisoning, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseRecruitingNot stated2017-04-27NCT03131427