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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Safety, Pharmacokinetics (PK), and Efficacy of Garetosmab in Children and Adolescents With Fibrodysplasia Ossificans Progressiva (FOP)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Ossification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, fibrodysplasia ossificans progressiva, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansNot yet recruitingPhase 32026-10-08NCT07559513
A Study to Document and to Further Describe Long-term Safety and Effectiveness of Palovarotene in Participants With Fibrodysplasia Ossificans Progressiva (FOP)fibrodysplasia ossificans progressiva, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansRecruitingNot stated2026-10-01NCT06089616
Saracatinib Trial TO Prevent FOPfibrodysplasia ossificans progressiva, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansActive, not recruitingPhase 22026-09-02NCT04307953
IL1 Inhibition in FOPOssification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansRecruitingNot stated2026-08-06NCT06724562
A Study to Assess Safety, Tolerability and Efficacy of Garetosmab Versus Placebo Administered Intravenously (IV) in Adult Participants With Fibrodysplasia Ossificans Progressiva (FOP)Ossification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, fibrodysplasia ossificans progressiva, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansActive, not recruitingPhase 32026-07-17NCT05394116
To Assess the Efficacy, Safety, and Tolerability of INCB000928 in Participants With Fibrodysplasia Ossificans ProgressivaOssification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansRecruitingPhase 22026-05-22NCT05090891
The Fibrodysplasia Ossificans Progressiva (FOP) RegistryBone Diseases, Developmental, Foot Deformities, Hallux Valgus, Neoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, Ossification, Heterotopic, Osteochondroma, Pathologic Processes, Pathological Conditions, Signs and Symptoms, bone disorder, connective tissue neoplasm, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificans, neoplasm, osteochondrodysplasiaRecruitingNot stated2026-04-08NCT02745158
A Study of Andecaliximab in Participants With Fibrodysplasia Ossificans Progressiva (FOP)Foot Deformities, Hallux Valgus, Inflammation, Ossification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, fibrodysplasia ossificans progressiva, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificans, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 2 / Phase 32025-10-14NCT06508021