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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Teleneurology Assessment Program for Creutzfeldt-Jakob DiseaseCreutzfeldt Jacob disease, Infections, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, nervous system disorder, neurodegenerative disease, prion disease, psychiatric disorderRecruitingNot stated2026-09-25NCT07840547
A Trial of ALN-6457 in Adult Participants With Symptomatic Prion Disease (PrD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Creutzfeldt Jacob disease, Dyssomnias, Gerstmann-Straussler-Scheinker syndrome, Infections, Nutritional and Metabolic Diseases, Sleep Disorders, Intrinsic, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, fatal familial insomnia, hereditary disease, inherited neurodegenerative disorder, insomnia, metabolic disease, nervous system disorder, neurodegenerative disease, prion disease, proteostasis deficiencies, psychiatric disorder, sleep-wake disorderNot yet recruitingPhase 1 / Phase 22026-09-22NCT07832370
Promoting Goals-of-Care Discussions for Patients With Memory Problems and Their CaregiversAlzheimer disease, Arterial Occlusive Diseases, Chronic Disease, Cognition Disorders, Cognitive Dysfunction, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Creutzfeldt Jacob disease, Disease Attributes, Dyskinesias, Frontotemporal Lobar Degeneration, Huntington disease, Infections, Leukoencephalopathies, Lewy body dementia, Mixed Dementias, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, TDP-43 proteinopathy, arteriosclerosis disorder, basal ganglia disorder, brain disorder, cardiovascular disorder, central nervous system disorder, central nervous system infectious disorder, cerebrovascular disorder, choreatic disease, cognitive disorder, dementia, hereditary disease, inherited neurodegenerative disorder, intracranial arterial disease, intracranial arteriosclerosis, metabolic disease, movement disorder, nervous system disorder, neurodegenerative disease, parkinsonian disorder, prion disease, proteostasis deficiencies, psychiatric disorder, synucleinopathy, tauopathy, vascular dementia, vascular disorderActive, not recruitingNot applicable2026-09-21NCT05596760
PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717Infections, central nervous system disorder, central nervous system infectious disorder, nervous system disorder, neurodegenerative disease, prion diseaseActive, not recruitingPhase 1 / Phase 22026-09-18NCT06153966
PROSPECT Registry for Individuals at Risk for Genetic Prion DiseaseInfections, central nervous system disorder, central nervous system infectious disorder, nervous system disorder, neurodegenerative disease, prion diseaseRecruitingNot stated2026-09-16NCT07732608
Efavirenz for the Treatment of Creutzfeldt-Jakob DiseaseCreutzfeldt Jacob disease, Infections, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, nervous system disorder, prion disease, psychiatric disorderRecruitingPhase 32026-09-03NCT07482085
PrP-targeting siRNA Safety & Mechanism StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Creutzfeldt Jacob disease, Dyssomnias, Gerstmann-Straussler-Scheinker syndrome, Infections, Sleep Disorders, Intrinsic, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, fatal familial insomnia, hereditary disease, inherited neurodegenerative disorder, insomnia, nervous system disorder, neurodegenerative disease, prion disease, psychiatric disorder, sleep-wake disorderRecruitingPhase 12026-08-28NCT07444580
OBSERVE: Biomarkers in Individuals at Risk for Prion DiseaseCreutzfeldt Jacob disease, Dyssomnias, Infections, Sleep Disorders, Intrinsic, central nervous system disorder, central nervous system infectious disorder, fatal familial insomnia, insomnia, nervous system disorder, neurodegenerative disease, prion disease, sleep-wake disorderRecruitingNot stated2026-08-13NCT05124392
CLIME-CJD: A Multimodal StudyCreutzfeldt Jacob disease, Infections, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, nervous system disorder, neurodegenerative disease, prion disease, psychiatric disorderEnrolling by invitationNot stated2026-05-15NCT07589283
Platelet-Rich Plasma Injections From Cord Blood + Penile Traction vs. Penile Traction Alone in Patients With Peyronie's Disease. Open-label, Single-center Randomized StudyDyssomnias, Genital Diseases, Infections, Male Urogenital Diseases, Peyronie disease, Skin and Connective Tissue Diseases, Sleep Disorders, Intrinsic, Urogenital Diseases, central nervous system disorder, central nervous system infectious disorder, connective tissue disorder, fatal familial insomnia, insomnia, male reproductive system disorder, nervous system disorder, neurodegenerative disease, penile disorder, prion disease, sleep-wake disorderRecruitingNot applicable2025-06-08NCT07010900
A Natural History Study of Preclinical Genetic Creutzfeldt-Jakob Disease (CJD)Creutzfeldt Jacob disease, Infections, brain disorder, central nervous system disorder, central nervous system infectious disorder, cognitive disorder, dementia, nervous system disorder, neurodegenerative disease, prion disease, psychiatric disorderRecruitingNot stated2023-02-28NCT05746715