congenital generalized lipodystrophy
congenital generalized lipodystrophy
Explore linked clinical trials. Standard reference: MONDO:00065367 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, congenital generalized lipodystrophy, familial partial lipodystrophy, hereditary disease, inborn errors of metabolism, laminopathy, lipodystrophy, metabolic disease, skin disorder | Recruiting | Phase 3 | 2026-09-11 | NCT07220785 | |
| MEASuRE: Metreleptin Effectiveness And Safety Registry | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, acquired partial lipodystrophy, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, lipodystrophy, metabolic disease, partial lipodystrophy, skin disorder | Recruiting | Not stated | 2026-07-16 | NCT02325674 | |
| 64Cu-GRIP B in Patients With Advanced Malignancies | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Male Urogenital Diseases, Neoplasms by Site, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, Urogenital Diseases, Urogenital Neoplasms, benign urinary system neoplasm, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, kidney cancer, kidney disorder, lipodystrophy, male reproductive organ cancer, male reproductive system disorder, metabolic disease, neoplasm, prostate cancer, prostate disorder, skin disorder, urethra neoplasm, urethral disorder, urinary system disorder | Recruiting | Phase 1 / Phase 2 | 2026-03-17 | NCT05888532 | |
| Granzyme B-targeted PET Imaging Monitoring Tumor Responses to Immunotherapy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, lipodystrophy, metabolic disease, skin disorder | Not yet recruiting | Not stated | 2025-04-08 | NCT06916442 | |
| The Value of PET Imaging Targeting Granzyme B in Predicting Efficacy and Prognosis in T-NK Cell Lymphoma | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lymphoma, Extranodal NK-T-Cell, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, T-cell non-Hodgkin lymphoma, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, lipodystrophy, lymphoma, metabolic disease, neoplasm, skin disorder | Not yet recruiting | Not stated | 2025-03-07 | NCT06863441 | |
| PET Imaging Targeting Granzyme B Predicts Immunotherapy Efficacy in Diffuse Large B-cell Lymphoma | B-cell neoplasm, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, congenital generalized lipodystrophy, diffuse large B-cell lymphoma, hereditary disease, immune system disorder, immunoproliferative disorder, inborn errors of metabolism, lipodystrophy, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, metabolic disease, neoplasm, skin disorder | Recruiting | Not stated | 2025-01-01 | NCT06755775 | |
| GzmB-PET/CT to Evaluate Neoadjuvant Therapy Efficacy in Breast Cancer | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neoplasms by Site, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, breast disorder, breast neoplasm, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, lipodystrophy, metabolic disease, neoplasm, skin disorder | Recruiting | Not stated | 2024-12-10 | NCT06725940 |