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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Evaluate ENERGI-F703EB Cream in Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, epidermolysis bullosa simplex, hereditary disease, hereditary skin disorder, junctional epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 22026-10-05NCT07858422
A Study to Assess the Incidence of Skin Cancers in Patients With Epidermolysis Bullosa Receiving FilsuvezCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, junctional epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-09-28NCT06423573
An Open Label Extension Safety Study to Evaluate SD-101 in Epidermolysis BullosaCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, epidermolysis bullosa, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseNot yet recruitingPhase 32026-09-09NCT07482813
Emerging Indications for Hyperbaric Oxygen TreatmentArterial Occlusive Diseases, Axonotmesis, Bacterial Infections and Mycoses, CNS demyelinating autoimmune disease, Clostridium Enterocolitis, Clostridium difficile colitis, Clostridium infectious disease, Cold Injury, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Conjunctival Diseases, Craniocerebral Trauma, Crohn disease, Crohn ileitis, Digestive System Diseases, Digestive System Fistula, Ear Diseases, Embolism and Thrombosis, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Fistula, Genital Diseases, Ileal Diseases, Infections, Invasive Fungal Infections, Male Urogenital Diseases, Necrosis, Neurologic Manifestations, Nonarteritic Anterior Ischemic Optic Neuropathy, Nutritional and Metabolic Diseases, Optic Neuropathy, Ischemic, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Raynaud disease, Rectovaginal Fistula, Sensation Disorders, Signs and Symptoms, Skin Abnormalities, Skin Ulcer, Skin and Connective Tissue Diseases, Urogenital Abnormalities, Urogenital Diseases, Vaginal Fistula, Venous Thrombosis, anal fistula, autoimmune disease, autoimmune disorder of the nervous system, bacterial infectious disease, bone disorder, branch retinal artery occlusion, calcinosis, calciphylaxis, calcium metabolic disease, cardiovascular disorder, central retinal vein occlusion, colitis, colonic disorder, cranial nerve neuropathy, decubitus ulcer, demyelinating disease, digestive system disorder, enteritis, enterocolitis, epidermolysis bullosa, eye disorder, female reproductive system disorder, frostbite, fungal infectious disease, gastroenteritis, graft versus host disease, gram-positive bacterial infections, hearing disorder, hereditary disease, hereditary skin disorder, hypospadias, immune system disorder, inclusion body myositis, inflammatory bowel disease, injury, intestinal disorder, intestinal fistula, livedoid vasculopathy, male reproductive system disorder, malignant otitis externa, metabolic disease, multiple sclerosis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, nervous system injury, neuromuscular disease, optic nerve disorder, osteonecrosis, otorhinolaryngologic disease, penile disorder, peripheral vascular disease, pouchitis, prosthesis-related infectious disease, pterygium, pyoderma, pyoderma gangrenosum, rectal disorder, retinal artery occlusion, retinal disorder, retinal vein occlusion, skin disorder, skin vascular disease, thrombotic disease, tinnitus, ulcerative colitis, vaginal disorder, vascular disorder, vesiculobullous skin diseaseNot yet recruitingPhase 42026-09-09NCT07240649
Efficacy and Safety Study to Evaluate SD-101 in Epidermolysis BullosaCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Abnormalities, Skin Manifestations, Skin and Connective Tissue Diseases, epidermolysis bullosa, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseRecruitingPhase 32026-09-04NCT07482787
Impact of Body Positioning on EndoFLIP Measurements: A Comparative Study of Supine and Left Lateral Decubitus PositionsCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deglutition Disorders, Digestive System Diseases, Eosinophilia, Esophageal Stenosis, Esophageal Stricture, Hemic and Lymphatic Diseases, Hypersensitivity, Immediate, Pharyngeal Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, achalasia, digestive system disorder, dyskinesia of esophagus, eosinophilic esophagitis, epidermolysis bullosa, esophageal disorder, esophagitis, gastroenteritis, hematologic disorder, hereditary disease, hereditary skin disorder, immune system disorder, leukocyte disorder, otorhinolaryngologic disease, skin disorder, vesiculobullous skin diseaseRecruitingNot applicable2026-08-24NCT07780981
A Phase II, Placebo Controlled, Clinical Trial of Topical TolaSure Targeting Aggregated Mutant Keratin in Epidermolysis Bullosa SimplexCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, epidermolysis bullosa, epidermolysis bullosa simplex, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseRecruitingPhase 22026-08-13NCT07027345
A Phase 2 Study of TCP-25 Gel in Patients With Epidermolysis Bullosa, STEP-studyCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, junctional epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 22026-08-12NCT06594393
Filsuvez in Moderate-to-Severe Epidermolysis Bullosa SimplexCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, epidermolysis bullosa, epidermolysis bullosa simplex, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseNot yet recruitingPhase 22026-08-10NCT07756138
Phase 4 Master Protocol for Patients Prescribed Prademagene Zamikeracel for the Treatment of WoundsCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseNot yet recruitingPhase 42026-08-06NCT07717736
Curcumin-Based Photodynamic Therapy in Epidermolysis Bullosa: Wound Healing, Quality of Life, and Salivary BiomarkersCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 42026-07-16NCT07596927
A Long-Term Safety Follow-up Registry for Patients Who Received Treatment With Prademagene Zamikeracel for Recessive Dystrophic Epidermolysis Bullosa (RDEB) in the Post-Marketing SettingCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-07-14NCT07700966
An International, Multicenter, Randomized, Double-Blind, Parallel Group, Vehicle-Controlled, Phase 2/3 Study With Open-Label Extension Evaluating the Efficacy and Safety of Diacerein 1% Ointment for the Treatment of Generalized Epidermolysis Bullosa Simplex (EBS)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, epidermolysis bullosa, epidermolysis bullosa simplex, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 2 / Phase 32026-07-09NCT06073132
Treatment of Dysphagia in Patients With Dystrophic Epidermolysis Bullosa With Budesonide: a Retrospective Bicentric Study Nice - Paris St Louis / Necker (EBUDE Study)Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deglutition Disorders, Digestive System Diseases, Esophageal Stenosis, Pharyngeal Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, digestive system disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, esophageal disorder, hereditary disease, hereditary skin disorder, otorhinolaryngologic disease, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseNot yet recruitingNot applicable2026-07-06NCT07684105
Targeting Collagen VII Antibodies in Bullous Diseases Using Efgartigimod IV (VYVGART)Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseNot yet recruitingPhase 1 / Phase 22026-05-05NCT07011589
Targeting Collagen VII Antibodies With IV IgG in Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 1 / Phase 22026-05-05NCT06834035
Repurposing Dupilumab for Management of Pruritic Genetic Inflammatory Skin DisordersCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Abnormalities, Skin Manifestations, Skin and Connective Tissue Diseases, epidermolysis bullosa, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorder, vesiculobullous skin diseaseRecruitingEarly phase 12026-05-01NCT05649098
Characteristics of Patients With Recessive Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-04-24NCT01019148
Self-Assembled Skin Substitute for the Treatment of Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingEarly phase 12026-03-19NCT04171661
GMEB-SASS: A Gene-Modified Skin Substitute for RDEB TreatmentCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 1 / Phase 22026-03-18NCT07193134
A Study of FCX-007 for Recessive Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 32026-03-18NCT04213261
Evaluation of D-Fi for the Treatment of Wounds Due to DEBCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 32026-03-13NCT06892639
A Study Comparing KB803 and Matched Placebo in Patients With Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, nervous system disorder, nervous system injury, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 32026-03-12NCT07016750
Ex Vivo Gene Therapy Clinical Trial for RDEB Using Genetically Corrected Autologous Skin Equivalent GraftsCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 1 / Phase 22026-02-12NCT04186650
Thera-Clean® Microbubbles System in Patients With Skin DiseasesCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypersensitivity, Immediate, Infant, Newborn, Diseases, Skin Abnormalities, Skin Diseases, Eczematous, Skin Diseases, Papulosquamous, Skin and Connective Tissue Diseases, atopic eczema, dermatitis, epidermolysis bullosa, hereditary disease, hereditary skin disorder, ichthyosis, immune system disorder, keratosis, psoriasis, skin disorder, vesiculobullous skin diseaseEnrolling by invitationEarly phase 12026-02-03NCT07050810