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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS)Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingPhase 32026-10-01NCT04958265
Collection of Human Samples to Study Hairy Cell and Other Leukemias, and to Develop Recombinant Immunotoxins for Cancer TreatmentB-cell chronic lymphocytic leukemia, Chronic Disease, Cytopenia, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Leukemia, B-Cell, Male Urogenital Diseases, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Precursor T-Cell Lymphoblastic Leukemia-Lymphoma, T-cell non-Hodgkin lymphoma, Urogenital Diseases, anemia, blood platelet disease, hairy cell leukemia, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, immune system disorder, immunoproliferative disorder, kidney disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, primary cutaneous T-cell non-Hodgkin lymphoma, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2026-09-22NCT01087333
Ravulizumab Outcomes in Polish Patients With aHUSCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2026-09-15NCT07399730
Anrikefon vs Nalfurafine for Sleep Quality in Hemodialysis Patients With CKD-aPBronchiolitis Obliterans, Chronic Disease, Chronic Kidney Diseases, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, chronic renal failure syndrome, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, kidney disorder, kidney failure, lung disorder, obstructive lung disease, respiratory system disorder, uremia, urinary system disorderRecruitingPhase 42026-08-25NCT07380113
Incremental Hemodialysis for Veterans in the First Year of Dialysis (IncHVets)Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, uremia, urinary system disorderRecruitingNot applicable2026-08-20NCT05465044
A Prospective, Non-interventional, Observational Study of Presentation, Treatment Patterns and Outcomes in Atypical Hemolytic Uremic Syndrome PatientsCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingNot stated2026-07-22NCT06099236
A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Adult and Adolescent Participants With Atypical Hemolytic Uremic Syndrome (aHUS)Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingPhase 32026-07-21NCT04861259
Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUSCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, glomerulonephritis, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, immune system disorder, kidney disorder, membranoproliferative glomerulonephritis, nephritis, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingPhase 32026-06-04NCT05795140
Hyperhydration in Children With Shiga Toxin-Producing E. Coli InfectionBacterial Infections and Mycoses, Cytopenia, Disease Attributes, Emergencies, Enterobacteriaceae Infections, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Infections, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, acute kidney injury, anemia, bacterial infectious disease, blood platelet disease, escherichia coli infection, gram-negative bacterial infections, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, kidney failure, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot applicable2026-05-18NCT05219110
Efficacy and Safety of Switching From Anti-C5 Antibody Treatment to Iptacopan Treatment in Study Participants With Atypical Hemolytic Uremic Syndrome (aHUS)Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingPhase 32026-04-29NCT05935215
A Self-Controlled Study on the Treatment of Restless Legs Syndrome in Uremia With DipyridamoleDyssomnias, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Parasomnias, Sleep Disorders, Intrinsic, Urogenital Diseases, kidney disorder, nervous system disorder, psychiatric disorder, restless legs syndrome, sleep-wake disorder, uremia, urinary system disorderRecruitingPhase 2 / Phase 32026-04-22NCT07199504
ICHARUS: Italian Cooperative HemoAdsorption Study for Relief of Uremic SymptomsBronchiolitis Obliterans, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, kidney disorder, lung disorder, obstructive lung disease, respiratory system disorder, uremia, urinary system disorderRecruitingNot stated2026-04-21NCT07522008
Post-Marketing Clinical Study of Ravulizumab in Participants With Clinical aHUSCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingPhase 42026-04-20NCT07308574
Study of Ultomiris® (Ravulizumab) Safety in PregnancyCNS demyelinating autoimmune disease, Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, Male Urogenital Diseases, Neoplasms by Site, Paraneoplastic Syndromes, Nervous System, Urogenital Diseases, acute transverse myelitis, anemia, atypical hemolytic-uremic syndrome, autoimmune disease, autoimmune disorder of the nervous system, blood platelet disease, bone marrow disorder, cranial nerve neuropathy, demyelinating disease, eye disorder, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, immune system disorder, kidney disorder, myasthenia gravis, myelodysplastic syndrome, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, neuromyelitis optica, optic nerve disorder, optic neuritis, paraneoplastic syndrome, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2026-04-16NCT06312644
Study of NM8074 in Patients With aHUS With Evidence of Ongoing Thrombotic MicroangiopathyCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderNot yet recruitingPhase 22026-04-13NCT05684159
Expanded Hemodialysis Versus High-Volume Online Hemodiafiltration for Uremic Toxin RemovalBronchiolitis Obliterans, Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, chronic renal failure syndrome, cryptogenic organizing pneumonia, end stage renal failure, graft versus host disease, immune system disorder, kidney disorder, kidney failure, lung disorder, obstructive lung disease, respiratory system disorder, uremia, urinary system disorderNot yet recruitingNot applicable2026-03-24NCT07348536
Developing a Pipeline to Employ RNA-Seq as a Complementary Diagnostic Tool in Rare DiseasesAbnormalities, Multiple, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, autosomal dominant polycystic kidney disease, blood platelet disease, cystic kidney disease, glomerulonephritis, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, hereditary disease, immune system disorder, kidney disorder, membranoproliferative glomerulonephritis, nephritis, polycystic kidney disease, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot applicable2026-03-23NCT05996731
New Analytic Tools for aHUS and C3G DiagnosisCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, blood platelet disease, glomerulonephritis, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, immune system disorder, kidney disorder, membranoproliferative glomerulonephritis, nephritis, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingNot applicable2026-03-23NCT05985122
Efficacy of INM004 in Children With STEC-HUSCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingPhase 32026-01-15NCT06389474
Studies on Adsorption International Learning Initiative GlobalBronchiolitis Obliterans, Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Infections, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Toxemia, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, chronic renal failure syndrome, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, kidney disorder, kidney failure, lung disorder, obstructive lung disease, respiratory system disorder, uremia, urinary system disorderRecruitingNot applicable2025-12-10NCT07123909
Complement Prospective Evaluation of Thrombotic Microangiopathy on EndotheliumCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2025-10-01NCT04745195
Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized TherapyCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot applicable2025-09-29NCT05805202
Dynamic Breath VOC Profiling as a Non-invasive Tool to Assess Hemodialysis AdequacyBronchiolitis Obliterans, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, kidney disorder, lung disorder, obstructive lung disease, respiratory system disorder, uremia, urinary system disorderNot yet recruitingNot stated2025-09-24NCT07189741
Atypical Hemolytic-Uremic Syndrome (aHUS) RegistryCytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderRecruitingNot stated2025-09-16NCT01522183
Timing of Renal Replacement Therapy in the Critically Ill PatientsCritical Illness, Disease Attributes, Edema, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, acute kidney injury, kidney disorder, kidney failure, uremia, urinary system disorderRecruitingNot stated2025-09-03NCT03629977