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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Clinical Trial Evaluating the Impact of an Intensive Rehabilitation Program Combined With Tendon Vibratory Stimulation on Functional Balance in Individuals With Charcot-Marie-Tooth Disease Type 1ACharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingNot applicable2026-08-03NCT07726043
Evaluate the Safety and Efficacy of EN001 in Patients With Charcot-Marie-Tooth Disease Type 1A(CMT1A) (Phase 1b: Open-label, Dose-escalation, Single-center; Phase 2a: Randomized, Double-blind, Placebo-controlled, Multicenter)Charcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingPhase 1 / Phase 22026-05-26NCT06328712
AUTONOMOUS DISORDERS IN CMTCharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingNot stated2026-05-06NCT07570446
A Multi-omic Approach to the Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease (CMT1A)Charcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Models, Animal, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, non-human animal disease, peripheral nervous system disorder, polyneuropathyRecruitingNot stated2026-04-13NCT07476365
Studying Nerve Function and Structure in Charcot-Marie-Tooth Disease, Anti-MAG Neuropathy and CIDPCharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease X-linked dominant 1, Charcot-Marie-Tooth disease type 1A, Charcot-Marie-Tooth disease type 4B2, Charcot-Marie-Tooth disease type 4D, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, autoimmune disease, autoimmune disorder of the nervous system, central nervous system malformation, chronic inflammatory demyelinating polyradiculoneuropathy, demyelinating disease, hereditary disease, hereditary motor and sensory neuropathy, immune system disorder, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, polyneuropathy associated with IgM monoclonal gammapathy with anti-MAG, polyradiculoneuropathyRecruitingNot stated2026-03-10NCT07461896
Longitudinal Biomarkers With Selected Outcome Measures In CMTCharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingNot stated2026-03-09NCT06794489
Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A DiseaseCharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingNot applicable2025-07-03NCT07049588
Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and BiomarkersCharcot-Marie-Tooth disease, Charcot-Marie-Tooth disease type 1A, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyActive, not recruitingNot applicable2025-06-27NCT02596191