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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Adult and Juvenile MyositisSkin and Connective Tissue Diseases, connective tissue disorder, dermatomyositis, inclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, polymyositis, skin disorderRecruitingNot stated2026-09-24NCT00017914
Imaging Assessment of Swallowing and Speech Muscles in Inclusion Body MyositisAsthenia, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, inclusion body myositis, metabolic disease, motor neuron disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingNot stated2026-09-16NCT07823101
Emerging Indications for Hyperbaric Oxygen TreatmentArterial Occlusive Diseases, Axonotmesis, Bacterial Infections and Mycoses, CNS demyelinating autoimmune disease, Clostridium Enterocolitis, Clostridium difficile colitis, Clostridium infectious disease, Cold Injury, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Conjunctival Diseases, Craniocerebral Trauma, Crohn disease, Crohn ileitis, Digestive System Diseases, Digestive System Fistula, Ear Diseases, Embolism and Thrombosis, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Fistula, Genital Diseases, Ileal Diseases, Infections, Invasive Fungal Infections, Male Urogenital Diseases, Necrosis, Neurologic Manifestations, Nonarteritic Anterior Ischemic Optic Neuropathy, Nutritional and Metabolic Diseases, Optic Neuropathy, Ischemic, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Raynaud disease, Rectovaginal Fistula, Sensation Disorders, Signs and Symptoms, Skin Abnormalities, Skin Ulcer, Skin and Connective Tissue Diseases, Urogenital Abnormalities, Urogenital Diseases, Vaginal Fistula, Venous Thrombosis, anal fistula, autoimmune disease, autoimmune disorder of the nervous system, bacterial infectious disease, bone disorder, branch retinal artery occlusion, calcinosis, calciphylaxis, calcium metabolic disease, cardiovascular disorder, central retinal vein occlusion, colitis, colonic disorder, cranial nerve neuropathy, decubitus ulcer, demyelinating disease, digestive system disorder, enteritis, enterocolitis, epidermolysis bullosa, eye disorder, female reproductive system disorder, frostbite, fungal infectious disease, gastroenteritis, graft versus host disease, gram-positive bacterial infections, hearing disorder, hereditary disease, hereditary skin disorder, hypospadias, immune system disorder, inclusion body myositis, inflammatory bowel disease, injury, intestinal disorder, intestinal fistula, livedoid vasculopathy, male reproductive system disorder, malignant otitis externa, metabolic disease, multiple sclerosis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, nervous system injury, neuromuscular disease, optic nerve disorder, osteonecrosis, otorhinolaryngologic disease, penile disorder, peripheral vascular disease, pouchitis, prosthesis-related infectious disease, pterygium, pyoderma, pyoderma gangrenosum, rectal disorder, retinal artery occlusion, retinal disorder, retinal vein occlusion, skin disorder, skin vascular disease, thrombotic disease, tinnitus, ulcerative colitis, vaginal disorder, vascular disorder, vesiculobullous skin diseaseNot yet recruitingPhase 42026-09-09NCT07240649
The Aim of the Study is to Characterize Patients Exhibiting Muscular Atrophy and Weakness Who Require a Muscle Biopsy for Diagnosis (IBM vs Atypical MND), Through an Innovative Technique Which Enables the Evaluation of the Neuromuscular Junction Involvement in Each ConditionNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, inclusion body myositis, metabolic disease, motor neuron disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderActive, not recruitingNot stated2026-09-01NCT07796776
Monitoring Biomarker for Detecting Change in Physical Activity and Limb Function in Inclusion Body Myositis Over Timeinclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseActive, not recruitingNot stated2026-06-29NCT06153108
Ruxolitinib Treatment in Inclusion Body MyositisInclusion Body Myopathy, Sporadic, inclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseRecruitingPhase 22026-05-29NCT06536166
Sporadic Inclusion Body Myositis Natural History Studyinclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseActive, not recruitingNot stated2026-05-27NCT05046821
IBM Dietary Surveillance Studyinclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseNot yet recruitingNot stated2026-04-17NCT07535996
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Charcot-Marie-Tooth disease, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Infections, Lambert-Eaton myasthenic syndrome, Lysosomal Storage Diseases, Nervous System, Muscular Disorders, Atrophic, Neoplasms by Site, Neuroinflammatory Diseases, Nutritional and Metabolic Diseases, Paraneoplastic Syndromes, Nervous System, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Picornaviridae infectious disease, RNA Virus Infections, TDP-43 proteinopathy, amyotrophic lateral sclerosis, autoimmune disease, autoimmune disorder of the nervous system, autonomic nervous system disorder, brain disorder, central nervous system disorder, central nervous system infectious disorder, central nervous system malformation, centronuclear myopathy, chronic inflammatory demyelinating polyradiculoneuropathy, congenital structural myopathy, demyelinating disease, disorder of glycogen metabolism, enterovirus infectious disease, facioscapulohumeral muscular dystrophy, glycogen storage disease II, hereditary disease, hereditary motor and sensory neuropathy, hereditary spastic paraplegia, immune system disorder, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, inborn mitochondrial myopathy, inclusion body myositis, inherited neurodegenerative disorder, lateral sclerosis, lysosomal storage disease, metabolic disease, motor neuron disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myasthenia gravis, myelitis, myositis disease, nemaline myopathy, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, orthostatic intolerance, paraneoplastic syndrome, peripheral nervous system disorder, poliomyelitis, polyneuropathy, polyradiculoneuropathy, postpoliomyelitis syndrome, primary dysautonomia, progressive muscular atrophy, proteostasis deficiencies, spinal cord disorder, spinal muscular atrophy, viral infectious diseaseRecruitingNot applicable2026-03-17NCT07478172
MIHRA - Patient-Rooted Insights for Shaping Myositis Science (PRISMS)Dermatomyositis, Childhood Type, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Skin and Connective Tissue Diseases, acquired idiopathic inflammatory myopathy, connective tissue disorder, dermatomyositis, immune-mediated necrotizing myopathy, inclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, polymyositis, skin disorderRecruitingNot stated2026-01-28NCT07374107
Efficacy and Safety of Pozelimab and Cemdisiran Combination Therapy in Patients With Sporadic Inclusion Body Myositisacquired idiopathic inflammatory myopathy, inclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseRecruitingEarly phase 12026-01-16NCT06479863
Phase III Trial of Sirolimus in IBMinclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-01-14NCT04789070
Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular DisordersBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Friedreich ataxia, Guillain-Barre syndrome, Lambert-Eaton myasthenic syndrome, Lysosomal Storage Diseases, Nervous System, Muscular Disorders, Atrophic, Neoplasms by Site, Nutritional and Metabolic Diseases, Paraneoplastic Syndromes, Nervous System, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Post-Infectious Disorders, Spinocerebellar Degenerations, TDP-43 proteinopathy, amyotrophic lateral sclerosis, autoimmune disease, autoimmune disorder of the nervous system, brain disorder, central nervous system disorder, central nervous system malformation, cerebellar disorder, chronic inflammatory demyelinating polyradiculoneuropathy, demyelinating disease, disorder of glycogen metabolism, facioscapulohumeral muscular dystrophy, glycogen storage disease II, hereditary disease, hereditary motor and sensory neuropathy, immune system disorder, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, inclusion body myositis, inherited neurodegenerative disorder, lysosomal storage disease, metabolic disease, motor neuron disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myasthenia gravis, myositis disease, myotonic dystrophy, myotonic syndrome, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, paraneoplastic syndrome, peripheral nervous system disorder, polyneuropathy, polyradiculoneuropathy, proteostasis deficiencies, spinal cord disorder, spinal muscular atrophyEnrolling by invitationNot stated2025-09-10NCT06605612
Long-term Extension Study of Ulviprubart (ABC008) in Subjects With Inclusion Body Myositisinclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 2 / Phase 32025-07-28NCT06450886
The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Friedreich ataxia, Guillain-Barre syndrome, Lambert-Eaton myasthenic syndrome, Lysosomal Storage Diseases, Nervous System, Muscular Disorders, Atrophic, Myotonic Dystrophy 2, Neoplasms by Site, Nutritional and Metabolic Diseases, Paraneoplastic Syndromes, Nervous System, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Post-Infectious Disorders, Spinocerebellar Degenerations, autoimmune disease, autoimmune disorder of the nervous system, brain disorder, central nervous system disorder, central nervous system malformation, cerebellar disorder, chronic inflammatory demyelinating polyradiculoneuropathy, demyelinating disease, disorder of glycogen metabolism, facioscapulohumeral muscular dystrophy, glycogen storage disease II, hereditary disease, hereditary motor and sensory neuropathy, immune system disorder, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, inclusion body myositis, inherited neurodegenerative disorder, limb-girdle muscular dystrophy, lysosomal storage disease, metabolic disease, motor neuron disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myasthenia gravis, myositis disease, myotonic dystrophy, myotonic syndrome, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, paraneoplastic syndrome, peripheral nervous system disorder, polyneuropathy, polyradiculoneuropathy, spinal cord disorder, spinal muscular atrophyEnrolling by invitationNot applicable2025-07-18NCT07072676
Investigating Genes in Patients With Polymyositis and DermatomyositisSkin and Connective Tissue Diseases, connective tissue disorder, dermatomyositis, inclusion body myositis, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, polymyositis, skin disorderActive, not recruitingNot stated2023-04-05NCT01171573