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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy for Crigler Najjar Syndrome Type I (AlphaCN)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 1 / Phase 22025-01-13NCT06641154
Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 22024-12-03NCT06518005
Gene Therapy for Severe Crigler Najjar SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Crigler-Najjar syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, metabolic diseaseRecruitingNot applicable2023-03-28NCT03466463