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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05444257
Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508delCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05331183
Bacteriophages for Adults With Cystic Fibrosis and Chronic Achromobacter Lung InfectionCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 12026-10-08NCT07275905
Role of Genetic Factors in the Development of Lung DiseaseCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Fibrosis, Hemic and Lymphatic Diseases, Hypersensitivity, Delayed, Hypersensitivity, Immediate, Infant, Newborn, Diseases, Malformations of Cortical Development, Group I, Neoplasms, Multiple Primary, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiratory Hypersensitivity, Subcutaneous Emphysema, alpha 1-antitrypsin deficiency, asthma, bronchial disorder, central nervous system malformation, cerebral cortical dysplasia, cystic fibrosis, hamartoma, hereditary disease, hereditary neoplastic syndrome, immune system disorder, inherited neurodegenerative disorder, interstitial lung disease, liver disorder, lung disorder, lymphatic system disorder, lymphoproliferative syndrome, neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, obstructive lung disease, pancreas disorder, pulmonary emphysema, pulmonary fibrosis, pulmonary sarcoidosis, respiratory system disorder, sarcoidosis, tuberous sclerosisRecruitingNot stated2026-10-08NCT00001532
Health Outcomes of Parents With Cystic Fibrosis-Aim 2Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-10-07NCT06296394
Regional Phenotyping of CF and Non-CF BronchiectasisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-10-07NCT04793867
Phase 2 Study to Assess the Safety and Efficacy of ANG003Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, exocrine pancreatic insufficiency, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 22026-10-06NCT07450547
Acoustic Waveform Respiratory EvaluationAbnormalities, Multiple, Chronic Disease, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, Hypersensitivity, Immediate, Infant, Newborn, Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiratory Hypersensitivity, asthma, bronchial disorder, bronchiectasis, chronic obstructive pulmonary disease, cystic fibrosis, hereditary disease, immune system disorder, lung disorder, obstructive lung disease, otorhinolaryngologic disease, pancreas disorder, primary ciliary dyskinesia, respiratory system disorderRecruitingNot applicable2026-10-05NCT06512064
Exercise in Child HealthCOVID-19, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronaviridae Infections, Digestive System Diseases, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, anemia, cystic fibrosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, lung disorder, pancreas disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, sickle cell disease, viral infectious disease, viral pneumoniaRecruitingNot applicable2026-10-02NCT05359991
Natural History of Noncirrhotic Portal HypertensionCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hypertrophy, Idiopathic Noncirrhotic Portal Hypertension, Infant, Newborn, Diseases, Male Urogenital Diseases, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Sex Chromosome Disorders, Splenomegaly, Turner syndrome, Urogenital Abnormalities, Urogenital Diseases, cardiovascular disorder, chromosomal disorder, congenital heart disease, cystic fibrosis, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, heart disorder, hereditary disease, immune system disorder, inborn error of immunity, isolated congenital hepatic fibrosis, liver disorder, lung disorder, pancreas disorder, portal hypertension, respiratory system disorder, sex chromosome disorder of sex development, varicose disease, vascular disorderRecruitingNot stated2026-10-02NCT02417740
Natural History of BronchiectasisAbnormalities, Multiple, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, autoimmune disease, bronchial disorder, bronchiectasis, common variable immunodeficiency, cystic fibrosis, hereditary disease, immune system disorder, inborn error of immunity, lung disorder, otorhinolaryngologic disease, pancreas disorder, primary ciliary dyskinesia, respiratory system disorderRecruitingNot stated2026-10-02NCT00943514
Reproducibility of Continuous Glucose Monitoring (CGM) in the Assessment of Glucose Metabolism Disorders in Children With Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, cystic fibrosis, glucose metabolism disease, hereditary disease, lung disorder, metabolic disease, pancreas disorder, respiratory system disorderNot yet recruitingNot applicable2026-10-01NCT07851831
A Study to Evaluate Safety and Explore Efficacy of New Lipase NHS7108 in Adult Participants With Exocrine Pancreatic Insufficiency.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, exocrine pancreatic insufficiency, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 22026-10-01NCT07559175
Safety and Efficacy of Inhaled BMD003 (CFTR mRNA) in Chinese Cystic Fibrosis Patients Aged ≥12 YearsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingEarly phase 12026-10-01NCT07485543
A Prospective, Single-center, Open-label Study of Inhaled BMD003 (CFTR mRNA) in Chinese Adults With Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingEarly phase 12026-10-01NCT06963008
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-272 in Healthy ParticipantsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 12026-09-23NCT07437105
BEGIN Novel ImagiNG BiomarkersCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 42026-09-22NCT05517655
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-581 in Healthy ParticipantsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingPhase 12026-09-21NCT07283770
Nutrition Supplement for Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderNot yet recruitingNot applicable2026-09-21NCT07163078
Establishing Personalized Phage Therapy and Its Comparative Cost in Difficult-to-treat Infections (EPHICACI)Bacterial Infections and Mycoses, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, Suppuration, bacterial infectious disease, bronchial disorder, bronchiectasis, cystic fibrosis, disease, hereditary disease, hidradenitis, hidradenitis suppurativa, lung disorder, pancreas disorder, respiratory system disorder, skin disease caused by bacterial infection, skin disorder, skin disorder caused by infection, sweat gland disorderRecruitingNot stated2026-09-21NCT06368388
SGLT2 Inhibitor Therapy in Cystic Fibrosis-related DiabetesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, cystic fibrosis-related diabetes, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 2 / Phase 32026-09-21NCT06149793
French Validation of the AdT-Physio ScaleCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-09-18NCT06273566
Global Utilization And Registry Database for Improved preservAtion of doNor LUNGsChronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, Fibrosis, Infant, Newborn, Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, chronic obstructive pulmonary disease, cystic fibrosis, hereditary disease, interstitial lung disease, lung disorder, obstructive lung disease, pancreas disorder, pulmonary arterial hypertension, pulmonary emphysema, pulmonary fibrosis, pulmonary hypertension, respiratory system disorderEnrolling by invitationNot stated2026-09-18NCT04930289
ATUSA Ultrasound Diagnostic Imaging for Breast Lesions Evaluation (AUDIBLE) - iSono HealthCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Mastodynia, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Connective and Soft Tissue, Neoplasms, Fibrous Tissue, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin and Connective Tissue Diseases, breast cancer, breast disorder, breast fibroadenoma, breast neoplasm, connective tissue neoplasm, cystic fibrosis, epithelial neoplasm, fibroepithelial neoplasm, hereditary disease, lung disorder, neoplasm, pancreas disorder, respiratory system disorder, skin disorderRecruitingNot stated2026-09-17NCT07505797
Genetics of Insulin and Incretins in Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-09-16NCT01852448