Riley-Day syndrome | ClinicalTrials HQ

View definition

4 results · Page 1 of 1

Swipe the table sideways for more columns.

Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia	Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Riley-Day syndrome, autonomic nervous system disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, primary dysautonomia	Enrolling by invitation	Phase 2	2026-04-13		NCT06148311
Pilot Study of Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia	Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Riley-Day syndrome, autonomic nervous system disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, primary dysautonomia	Active, not recruiting	Phase 2	2026-03-04		NCT06128356
The Natural History of Familial Dysautonomia	Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Riley-Day syndrome, autonomic nervous system disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, primary dysautonomia	Recruiting	Not stated	2025-11-10		NCT03920774
Development of IPS from Donated Somatic Cells of Patients with Neurological Diseases	Alzheimer disease, Cognition Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Dyskinesias, Eye Diseases, Hereditary, Huntington disease, Muscular Disorders, Atrophic, Neurologic Manifestations, Nutritional and Metabolic Diseases, Parkinson disease, Primary Immunodeficiency Diseases, Riley-Day syndrome, Spinocerebellar Ataxias, TDP-43 proteinopathy, amyotrophic lateral sclerosis, atactic disorder, non-human animal, ataxia telangiectasia, autonomic nervous system disorder, basal ganglia disorder, brain disorder, cardiovascular disorder, central nervous system disorder, central nervous system malformation, cerebellar ataxia, cerebellar disorder, choreatic disease, cognitive disorder, dementia, eye disorder, hereditary disease, hereditary sensory and autonomic neuropathy, immune system disorder, inborn error of immunity, inherited neurodegenerative disorder, inherited retinal dystrophy, macular degeneration, metabolic disease, motor neuron disorder, movement disorder, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neuromuscular disease, parkinsonian disorder, peripheral nervous system disorder, polyneuropathy, primary dysautonomia, proteostasis deficiencies, psychiatric disorder, retinal degeneration, retinal disorder, retinitis pigmentosa, spinal cord disorder, spinal muscular atrophy, synucleinopathy, tauopathy, telangiectasis, vascular disorder	Recruiting	Not stated	2025-03-04		NCT00874783