recessive dystrophic epidermolysis bullosa
recessive dystrophic epidermolysis bullosa
Explore linked clinical trials. Standard reference: MONDO:000917910 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Long-Term Safety Follow-up Registry for Patients Who Received Treatment With Prademagene Zamikeracel for Recessive Dystrophic Epidermolysis Bullosa (RDEB) in the Post-Marketing Setting | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Not stated | 2026-07-14 | NCT07700966 | |
| Treatment of Dysphagia in Patients With Dystrophic Epidermolysis Bullosa With Budesonide: a Retrospective Bicentric Study Nice - Paris St Louis / Necker (EBUDE Study) | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deglutition Disorders, Digestive System Diseases, Esophageal Stenosis, Pharyngeal Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, digestive system disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, esophageal disorder, hereditary disease, hereditary skin disorder, otorhinolaryngologic disease, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Not yet recruiting | Not applicable | 2026-07-06 | NCT07684105 | |
| Targeting Collagen VII Antibodies in Bullous Diseases Using Efgartigimod IV (VYVGART) | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Not yet recruiting | Phase 1 / Phase 2 | 2026-05-05 | NCT07011589 | |
| Targeting Collagen VII Antibodies With IV IgG in Dystrophic Epidermolysis Bullosa | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Phase 1 / Phase 2 | 2026-05-05 | NCT06834035 | |
| GMEB-SASS: A Gene-Modified Skin Substitute for RDEB Treatment | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Phase 1 / Phase 2 | 2026-03-18 | NCT07193134 | |
| A Study of FCX-007 for Recessive Dystrophic Epidermolysis Bullosa | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Active, not recruiting | Phase 3 | 2026-03-18 | NCT04213261 | |
| A Study Comparing KB803 and Matched Placebo in Patients With Dystrophic Epidermolysis Bullosa | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, nervous system disorder, nervous system injury, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Phase 3 | 2026-03-12 | NCT07016750 | |
| Pilot Study of ELK-003 Eye Drops for Treating Ocular Manifestations of Epidermolysis Bullosa | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, junctional epidermolysis bullosa, nervous system disorder, nervous system injury, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Active, not recruiting | Phase 1 | 2025-12-31 | NCT06713434 | |
| A Phase 3b Study for the Treatment of Dystrophic Epidermolysis Bullosa (DEB) in New and Previously EB-101 Treated Patients | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Active, not recruiting | Phase 3 | 2025-06-27 | NCT05725018 | |
| Long-Term Follow-up Protocol | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Not stated | 2021-06-08 | NCT04917887 |