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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-Term Safety Follow-up Registry for Patients Who Received Treatment With Prademagene Zamikeracel for Recessive Dystrophic Epidermolysis Bullosa (RDEB) in the Post-Marketing SettingCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2026-07-14NCT07700966
Treatment of Dysphagia in Patients With Dystrophic Epidermolysis Bullosa With Budesonide: a Retrospective Bicentric Study Nice - Paris St Louis / Necker (EBUDE Study)Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Deglutition Disorders, Digestive System Diseases, Esophageal Stenosis, Pharyngeal Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, digestive system disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, esophageal disorder, hereditary disease, hereditary skin disorder, otorhinolaryngologic disease, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseNot yet recruitingNot applicable2026-07-06NCT07684105
Targeting Collagen VII Antibodies in Bullous Diseases Using Efgartigimod IV (VYVGART)Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseNot yet recruitingPhase 1 / Phase 22026-05-05NCT07011589
Targeting Collagen VII Antibodies With IV IgG in Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, acquired epidermolysis bullosa, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 1 / Phase 22026-05-05NCT06834035
GMEB-SASS: A Gene-Modified Skin Substitute for RDEB TreatmentCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hallopeau-Siemens Disease, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 1 / Phase 22026-03-18NCT07193134
A Study of FCX-007 for Recessive Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 32026-03-18NCT04213261
A Study Comparing KB803 and Matched Placebo in Patients With Dystrophic Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, nervous system disorder, nervous system injury, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingPhase 32026-03-12NCT07016750
Pilot Study of ELK-003 Eye Drops for Treating Ocular Manifestations of Epidermolysis BullosaCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Corneal Injuries, Craniocerebral Trauma, Eye Injuries, Facial Injuries, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, corneal disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, eye disorder, hereditary disease, hereditary skin disorder, injury, junctional epidermolysis bullosa, nervous system disorder, nervous system injury, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 12025-12-31NCT06713434
A Phase 3b Study for the Treatment of Dystrophic Epidermolysis Bullosa (DEB) in New and Previously EB-101 Treated PatientsCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseActive, not recruitingPhase 32025-06-27NCT05725018
Long-Term Follow-up ProtocolCollagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, recessive dystrophic epidermolysis bullosa, skin disorder, vesiculobullous skin diseaseRecruitingNot stated2021-06-08NCT04917887