granulomatous disease, chronic, autosomal recessive, cytochrome b-positive, type 1
granulomatous disease, chronic, autosomal recessive, cytochrome b-positive, type 1
Explore linked clinical trials. Standard reference: MONDO:00093092 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| pCCLCHIM-p47 (Lentiviral Vector Transduced CD34 Plus Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD) | Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, X-linked disease, chronic granulomatous disease, granulomatous disease, chronic, autosomal recessive, cytochrome b-positive, type 1, hematologic disorder, hereditary disease, immune system disorder, inborn error of immunity, leukocyte disorder, phagocyte bactericidal dysfunction | Enrolling by invitation | Phase 1 / Phase 2 | 2026-09-15 | NCT06253507 | |
| Lentiviral Gene Therapy for p47 AR-CGD | granulomatous disease, chronic, autosomal recessive, cytochrome b-positive, type 1 | Recruiting | Phase 1 / Phase 2 | 2023-05-16 | NCT05207657 |