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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of Treosulfan-Based Conditioning for HSCT in Nijmegen Breakage SyndromeDNA repair disease, Nijmegen breakage syndrome, Nutritional and Metabolic Diseases, metabolic diseaseNot yet recruitingPhase 22026-01-05NCT07316595
Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage SyndromeDNA repair disease, Nijmegen breakage syndrome, Nutritional and Metabolic Diseases, metabolic diseaseRecruitingPhase 22024-01-10NCT06198842