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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
GBE Deficiency (GSD IV and APBD) Natural History StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, adult polyglucosan body disease, disorder of glycogen metabolism, glycogen storage disease due to glycogen branching enzyme deficiency, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, metabolic diseaseRecruitingNot stated2026-05-05NCT02683512