Becker muscular dystrophy
Becker muscular dystrophy
Explore linked clinical trials. Standard reference: MONDO:001031118 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Registry for Duchenne and Becker Muscular Dystrophy | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-10-08 | NCT07402122 | |
| Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Enrolling by invitation | Phase 2 | 2026-09-17 | NCT06066580 | |
| Defining Endpoints in Becker Muscular Dystrophy | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Active, not recruiting | Not stated | 2026-09-03 | NCT05257473 | |
| Multimodal Study About Absence of Dp140 in Becker Muscular Dystrophy: Brain-muscle Imaging, Cognition and Muscle Function | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Not yet recruiting | Not stated | 2026-07-31 | NCT07740057 | |
| Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-07-28 | NCT07674758 | |
| Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-06-24 | NCT07378553 | |
| Duchenne Electronic Health Record Study | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, neuromuscular disease caused by qualitative or quantitative defects of dystrophin | Recruiting | Not stated | 2026-05-27 | NCT07609394 | |
| The Duchenne Registry | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, neuromuscular disease caused by qualitative or quantitative defects of dystrophin | Recruiting | Not stated | 2026-05-08 | NCT02069756 | |
| Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders | Abnormalities, Multiple, Becker muscular dystrophy, Ciliopathies, Cognition Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Duchenne muscular dystrophy, Dyskinesias, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Huntington disease, Infant, Newborn, Diseases, Male Urogenital Diseases, Muscular Disorders, Atrophic, Neoplasms by Histologic Type, Neoplasms, Nerve Tissue, Neurobehavioral Manifestations, Neurologic Manifestations, Polycystic Kidney, Autosomal Recessive, Sex Chromosome Disorders, Urogenital Diseases, X-linked disease, X-linked hydrocephalus with stenosis of the aqueduct of Sylvius, anemia, basal ganglia disorder, blood coagulation disease, brain disorder, central nervous system disorder, choreatic disease, chromosomal disorder, coagulation protein disease, cognitive disorder, cystic fibrosis, cystic kidney disease, dementia, familial hemolytic anemia, fragile X syndrome, hematologic disorder, hemolytic anemia, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, hereditary neoplastic syndrome, inherited blood coagulation disorder, inherited hemoglobinopathy, inherited neurodegenerative disorder, intellectual disability, kidney disorder, lung disorder, movement disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, neoplasm, nerve sheath neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neurofibroma, neurofibromatosis, neurofibromatosis-Noonan syndrome, neuromuscular disease, pancreas disorder, polycystic kidney disease, proximal spinal muscular atrophy, psychiatric disorder, respiratory system disorder, sickle cell disease, urinary system disorder | Recruiting | Not stated | 2026-04-23 | NCT06147414 | |
| DMD Gene Variants and Cardiac Dysfunction in Young Males With Dystrophinopathies | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-04-07 | NCT07515235 | |
| A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Not yet recruiting | Not stated | 2026-04-06 | NCT07511920 | |
| Biomarker Development for Muscular Dystrophies | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, facioscapulohumeral muscular dystrophy, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular disease | Recruiting | Not stated | 2025-11-24 | NCT05019625 | |
| Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2025-10-15 | NCT01484678 | |
| Follow-up Study on Female Carriers With DMD Gene Variants | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Enrolling by invitation | Not stated | 2025-06-06 | NCT05715957 | |
| Muscle MRI Outlining of Neuromuscular Diseases Using Artificial Intelligence | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, Nutritional and Metabolic Diseases, X-linked disease, facioscapulohumeral muscular dystrophy, familial periodic paralysis, hereditary disease, hypokalemic periodic paralysis, inborn errors of metabolism, inborn metal metabolism disorder, metabolic disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Not yet recruiting | Not stated | 2025-04-08 | NCT06917430 | |
| Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies. | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Enrolling by invitation | Not applicable | 2025-04-01 | NCT06363526 | |
| Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases | Becker muscular dystrophy, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Lysosomal Storage Diseases, Nervous System, Muscular Disorders, Atrophic, Nutritional and Metabolic Diseases, Thomsen and Becker disease, X-linked disease, brain disorder, central nervous system disorder, congenital myopathy, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal storage disease, metabolic disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular disease | Recruiting | Not applicable | 2025-02-18 | NCT06833489 | |
| Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Active, not recruiting | Not stated | 2024-08-27 | NCT02972580 |