41 results · Page 1 of 2

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
HAELO: A Phase 3 Study to Evaluate NTLA-2002 in Participants With Hereditary Angioedema (HAE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 32026-10-08NCT06634420
Study of IV Human Plasma-derived C1 Esterase Inhibitor Concentrate in Patients With Congenital C1-INH Deficiency for Treatment and Pre-procedure Preventing of Acute Hereditary Angioedema AttacksEdema, Hypersensitivity, Immediate, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, immune system disorder, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-29NCT06361537
NTLA-2002 in Adults With Hereditary Angioedema (HAE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 1 / Phase 22026-09-25NCT05120830
Long-Term, Open-label Study of Oral Deucrictibant Extended-Release Tablet for Prophylaxis Against Angioedema Attacks in Adolescents and Adults With HAECongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderEnrolling by invitationPhase 32026-09-22NCT06679881
Study of Oral Deucrictibant XR Tablet for Prophylaxis and Deucrictibant Soft Capsule for On-Demand Treatment of Angioedema Attacks in Adults With Acquired Angioedema Due to C1 Inhibitor DeficiencyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, acquired angioedema, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-21NCT07266805
Safety and Effectiveness of Sebetralstat (KVD900) for Short-Term Prophylaxis Before Procedures in People With Hereditary Angioedema (KONTROL)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 42026-09-17NCT07654829
STOP-HAE: A Phase 3 Study of ADX-324 in HAECongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-10NCT06960213
Phase 3 Extension Study of ADX-324 in Participants With Hereditary Angioedema (HAE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-04NCT07428499
Donidalorsen Treatment in Children With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-02NCT07298447
ScATtEred Rare Disease Biobanks: a Model of Sample/Data Collection With susTainablE and Shared CriteriaAbnormalities, Multiple, Bone Diseases, Developmental, Cardiovascular Abnormalities, Cognition Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Dyskinesias, Huntington disease, Hypersensitivity, Immediate, Marfan syndrome, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Skin and Connective Tissue Diseases, angioedema, basal ganglia disorder, bone disorder, brain disorder, cardiovascular disorder, central nervous system disorder, choreatic disease, cognitive disorder, congenital heart disease, connective tissue disorder, dementia, heart disorder, hereditary disease, immune system disorder, inherited neurodegenerative disorder, movement disorder, musculoskeletal system disorder, nervous system disorder, neurodegenerative disease, psychiatric disorder, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot stated2026-08-27NCT06782230
Angioedema Biomarker Research StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Mast Cell Activation Disorders, Mastocytosis, Systemic, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, connective tissue neoplasm, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, indolent systemic mastocytosis, mastocytosis, neoplasm, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot stated2026-08-24NCT06210698
A Survey of Lanadelumab in Participants With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingNot stated2026-08-04NCT05397431
A Long-Term Study of Navenibart in Participants With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderEnrolling by invitationPhase 32026-07-30NCT07204938
Extension Study of Oral PHA-022121 for Acute Treatment of Angioedema Attacks in Patients With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Angioedema Type I, Hereditary Angioedema Type II, Hereditary Angioedema Types I and II, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary angioedema type 3, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderEnrolling by invitationPhase 2 / Phase 32026-07-21NCT05396105
A Study of Navenibart in Participants With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 32026-06-30NCT06842823
A Study of Takhzyro in Teenagers and Adults With Hereditary Angioedema (HAE) in South KoreaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderNot yet recruitingNot stated2026-06-18NCT07445087
A Study About the Diagnosis and Management of Hereditary Angioedema (HAE) in EgyptCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderNot yet recruitingNot stated2026-06-18NCT07218393
Safety, Tolerability, PK, PD of ADX-324 in Healthy Volunteers and Hereditary Angioedema PatientsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 1 / Phase 22026-06-16NCT05691361
A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot stated2026-06-03NCT07001280
A Study to Learn About the C1-Inhibitor Function as Diagnosis for Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot applicable2026-05-19NCT07293364
A Study of Lanadelumab in Teenagers and Adults With Hereditary Angioedema (HAE) in the Kingdom of Saudi ArabiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot stated2026-05-11NCT07263685
Deployment o the Multidisciplinary Prospective Cohort ImminentBehcet disease, CNS demyelinating autoimmune disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypersensitivity, Immediate, Respiratory Hypersensitivity, Skin Diseases, Eczematous, Skin Diseases, Papulosquamous, Skin and Connective Tissue Diseases, Spondylarthritis, Spondylarthropathies, Stomatognathic Diseases, angioedema, anterior uveitis, arthritic joint disease, arthropathy, asthma, atopic eczema, autoimmune disease, autoimmune disorder of the nervous system, bone disorder, bronchial disorder, cardiovascular disorder, connective tissue disorder, demyelinating disease, dermatitis, eye disorder, hereditary disease, hereditary periodic fever syndrome, hereditary skin disorder, immune system disorder, lung disorder, mouth disorder, multiple sclerosis, musculoskeletal system disorder, nervous system disorder, obstructive lung disease, panuveitis, psoriasis, psoriatic arthritis, respiratory system disorder, skin disorder, skin vascular disease, spondylitis, systemic sclerosis, urticaria, uveal disorder, uveitis, vascular disorder, vasculitis, vertebral column disorderRecruitingNot applicable2026-05-05NCT04334031
A Phase 2 in Adult Subjects With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 22026-04-17NCT06846398
Real-life Ecological Momentary Assessment of Lived Burden in Hereditary AngioEdemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingNot stated2026-03-04NCT07448181
Improving Deceased-Donor Kidney Transplant Outcomes Via a Single Intragraft Injection of C1 Esterase Inhibitor (IMPROVE TRIAL)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 22026-02-27NCT06919003