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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous DiseaseChronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, X-linked disease, chronic granulomatous disease, granulomatous disease, chronic, X-linked, hematologic disorder, hereditary disease, immune system disorder, inborn error of immunity, leukocyte disorder, phagocyte bactericidal dysfunctionActive, not recruitingPhase 1 / Phase 22026-08-21NCT06876363
Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous DiseaseChronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, X-linked disease, chronic granulomatous disease, granulomatous disease, chronic, X-linked, hematologic disorder, hereditary disease, immune system disorder, inborn error of immunity, leukocyte disorder, phagocyte bactericidal dysfunctionRecruitingPhase 1 / Phase 22026-08-13NCT06325709