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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-ThalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingPhase 22026-09-10NCT05664737
International Registry of Patients With Alpha ThalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingNot stated2026-09-02NCT04872179
Screening for Alpha Thalassemia in Healthy VolunteersCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaActive, not recruitingNot stated2026-04-24NCT02692872
Uncovering the Etiologies of Non-immune Hydrops FetalisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemiaEnrolling by invitationNot applicable2026-04-17NCT05528796
Hydrops: Diagnosing & Redefining Outcomes With Precision StudyCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Anomalies, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemiaActive, not recruitingNot applicable2026-04-17NCT03412760
Fetal Electrophysiologic Abnormalities in High-Risk Pregnancies Associated With Fetal DemiseArrhythmias, Cardiac, Brugada syndrome, Cardiac Conduction System Disease, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Death, Death, Sudden, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Death, Fetal Diseases, Hemic and Lymphatic Diseases, Hernia, Hernia, Abdominal, Infant Death, Infant, Newborn, Diseases, Musculoskeletal Abnormalities, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Sudden Infant Death, Urogenital Diseases, alpha thalassemia spectrum, anemia, cardiovascular disorder, congenital heart disease, fetal erythroblastosis, gastroschisis, heart disorder, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, musculoskeletal system disorder, neonatal anemia, pregnancy disorder, pregnancy disorder with abortive outcome, thalassemia, twin to twin transfusion syndromeRecruitingNot stated2026-03-04NCT03775954
Safety and Efficacy of RM-004 Cells for Hemoglobin H-Constant Spring DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingEarly phase 12024-06-03NCT06107400
Study of the Role of Genetic Modifiers in HemoglobinopathiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemiaRecruitingNot stated2024-03-20NCT05799118
RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, alpha thalassemia spectrum, anemia, beta thalassemia, bone marrow disorder, congenital dyserythropoietic anemia, cystinosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary anemia, hereditary disease, inborn errors of metabolism, inherited aplastic anemia, inherited hemoglobinopathy, iron metabolism disease, lysosomal storage disease, metabolic disease, myelodysplastic syndrome, pyruvate kinase deficiency of red cells, sickle cell disease, sideroblastic anemia, thalassemiaRecruitingNot stated2024-01-19NCT06213402
In-utero Hematopoietic Stem Cell Transplantation for the Treatment of Fetuses With Bart's Hydrops Fetalis SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemiaRecruitingNot applicable2023-04-12NCT05797272