alpha thalassemia spectrum
alpha thalassemia spectrum
Explore linked clinical trials. Standard reference: MONDO:001139910 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Phase 2 | 2026-09-10 | NCT05664737 | |
| International Registry of Patients With Alpha Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Not stated | 2026-09-02 | NCT04872179 | |
| Screening for Alpha Thalassemia in Healthy Volunteers | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Not stated | 2026-04-24 | NCT02692872 | |
| Uncovering the Etiologies of Non-immune Hydrops Fetalis | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemia | Enrolling by invitation | Not applicable | 2026-04-17 | NCT05528796 | |
| Hydrops: Diagnosing & Redefining Outcomes With Precision Study | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Anomalies, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemia | Active, not recruiting | Not applicable | 2026-04-17 | NCT03412760 | |
| Fetal Electrophysiologic Abnormalities in High-Risk Pregnancies Associated With Fetal Demise | Arrhythmias, Cardiac, Brugada syndrome, Cardiac Conduction System Disease, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Death, Death, Sudden, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Death, Fetal Diseases, Hemic and Lymphatic Diseases, Hernia, Hernia, Abdominal, Infant Death, Infant, Newborn, Diseases, Musculoskeletal Abnormalities, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Sudden Infant Death, Urogenital Diseases, alpha thalassemia spectrum, anemia, cardiovascular disorder, congenital heart disease, fetal erythroblastosis, gastroschisis, heart disorder, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, musculoskeletal system disorder, neonatal anemia, pregnancy disorder, pregnancy disorder with abortive outcome, thalassemia, twin to twin transfusion syndrome | Recruiting | Not stated | 2026-03-04 | NCT03775954 | |
| Safety and Efficacy of RM-004 Cells for Hemoglobin H-Constant Spring Disease | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Early phase 1 | 2024-06-03 | NCT06107400 | |
| Study of the Role of Genetic Modifiers in Hemoglobinopathies | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Recruiting | Not stated | 2024-03-20 | NCT05799118 | |
| RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, alpha thalassemia spectrum, anemia, beta thalassemia, bone marrow disorder, congenital dyserythropoietic anemia, cystinosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary anemia, hereditary disease, inborn errors of metabolism, inherited aplastic anemia, inherited hemoglobinopathy, iron metabolism disease, lysosomal storage disease, metabolic disease, myelodysplastic syndrome, pyruvate kinase deficiency of red cells, sickle cell disease, sideroblastic anemia, thalassemia | Recruiting | Not stated | 2024-01-19 | NCT06213402 | |
| In-utero Hematopoietic Stem Cell Transplantation for the Treatment of Fetuses With Bart's Hydrops Fetalis Syndrome | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Edema, Female Urogenital Diseases and Pregnancy Complications, Fetal Diseases, Hemic and Lymphatic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, alpha thalassemia spectrum, fetal erythroblastosis, hematologic disorder, hereditary disease, hydrops fetalis, immune system disorder, inherited hemoglobinopathy, pregnancy disorder, thalassemia | Recruiting | Not applicable | 2023-04-12 | NCT05797272 |