aromatic L-amino acid decarboxylase deficiency
aromatic L-amino acid decarboxylase deficiency
Explore linked clinical trials. Standard reference: MONDO:00120844 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients | aromatic L-amino acid decarboxylase deficiency | Recruiting | Phase 1 | 2026-08-27 | NCT02852213 | |
| A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants | aromatic L-amino acid decarboxylase deficiency | Active, not recruiting | Phase 2 | 2026-04-24 | NCT04903288 | |
| A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC Deficiency | aromatic L-amino acid decarboxylase deficiency | Active, not recruiting | Phase 2 / Phase 3 | 2026-04-21 | NCT06432140 | |
| An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency. | aromatic L-amino acid decarboxylase deficiency | Recruiting | Early phase 1 | 2023-03-13 | NCT05765981 |