4 results ยท Page 1 of 1

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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patientsaromatic L-amino acid decarboxylase deficiencyRecruitingPhase 12026-08-27NCT02852213
A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participantsaromatic L-amino acid decarboxylase deficiencyActive, not recruitingPhase 22026-04-24NCT04903288
A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC Deficiencyaromatic L-amino acid decarboxylase deficiencyActive, not recruitingPhase 2 / Phase 32026-04-21NCT06432140
An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.aromatic L-amino acid decarboxylase deficiencyRecruitingEarly phase 12023-03-13NCT05765981