3 results ยท Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Observing Disease Progression in a Patient With Hutchinson-Gilford Progeria Syndrome (HGPS)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, laminopathy, metabolic disease, progeroid syndromeNot yet recruitingNot stated2026-09-24NCT07839351
Creating Stem Cells From a Progeria Patient's Blood to Test Candidate Treatments in the LabCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, laminopathy, metabolic disease, progeroid syndromeNot yet recruitingNot stated2026-09-10NCT07803432
Phase I/II Trial of Everolimus in Combination With Lonafarnib in ProgeriaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, laminopathy, metabolic disease, progeroid syndromeEnrolling by invitationPhase 1 / Phase 22026-04-02NCT02579044