hereditary sensory and autonomic neuropathy
hereditary sensory and autonomic neuropathy
Explore linked clinical trials. Standard reference: MONDO:001536447 results · Page 1 of 2
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of ROC-101 in Patients With Pulmonary Arterial Hypertension (PAH) and Pulmonary Hypertension Associated With Interstitial Lung Disease (ILD-PH) (ROCSTAR STUDY) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, hypertensive disorder, inherited neurodegenerative disorder, interstitial lung disease, lung disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, vascular disorder | Recruiting | Phase 2 | 2026-10-08 | NCT07175038 | |
| Everolimus bAsed caLcineurin inhibiTor frEe immunosuppRession oNe Year AfTer lIver transplantatiON (ALTERNATION) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, liver disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 3 | 2026-10-05 | NCT07739914 | |
| Evaluating Efficacy of Tivozanib (AV-951) in Biliary Tract Cancers | Biliary Tract Neoplasms, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, adenocarcinoma, bile duct disorder, bile duct neoplasm, biliary tract disorder, carcinoma, central nervous system malformation, cholangiocarcinoma, epithelial neoplasm, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 1 / Phase 2 | 2026-10-02 | NCT04645160 | |
| NIS to Examine the Effectiveness of TDC in Patients With Metastatic Non-squamous NSCLC and High-risk Genetic Alterations | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Site, Thoracic Neoplasms, bronchial neoplasm, bronchogenic carcinoma, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, lung disorder, lung neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, non-small cell lung carcinoma, peripheral nervous system disorder, polyneuropathy, respiratory system disorder, respiratory tract neoplasm | Recruiting | Not stated | 2026-09-28 | NCT06494540 | |
| 9-ING-41 Combined With Retifanlimab, Plus Modified FOLFIRINOX for Patients With Advanced Pancreatic Adenocarcinoma (RiLEY) | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, pancreatic adenocarcinoma, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 1 | 2026-09-24 | NCT06896188 | |
| Study of ACR-2316 in Specific Advanced Solid Tumors | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 1 / Phase 2 | 2026-09-23 | NCT06667141 | |
| Carboplatin or Olaparib for BRcA Deficient Prostate Cancer | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fanconi anemia complementation group D1, Fanconi anemia complementation group N, Genital Diseases, Male Urogenital Diseases, Neoplasms by Site, Urogenital Diseases, Urogenital Neoplasms, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, male reproductive organ cancer, male reproductive system disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, prostate cancer, prostate disorder | Recruiting | Phase 2 | 2026-09-17 | NCT04038502 | |
| Postoperative Circulating Tumor DNA Monitoring in Stage I-III Driver-Mutant Colon Adenocarcinoma | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Neoplasms by Site, central nervous system malformation, colon adenocarcinoma, colonic disorder, colonic neoplasm, colorectal neoplasm, digestive system disorder, digestive system neoplasm, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, intestinal disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, rectal disorder | Recruiting | Not stated | 2026-09-02 | NCT07795528 | |
| A Study to Evaluate ARV-6723 Alone and With Pembrolizumab in Participants With Advanced Solid Tumors | Adnexal Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Virus Infections, Digestive System Diseases, Digestive System Neoplasms, Esophageal Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Head and Neck Neoplasms, Infections, Liver Neoplasms, Male Urogenital Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Otorhinolaryngologic Neoplasms, Pharyngeal Diseases, Skin and Connective Tissue Diseases, Stomatognathic Diseases, Thoracic Neoplasms, Tumor Virus Infections, Urogenital Diseases, Urogenital Neoplasms, Uterine Cervical Neoplasms, adenocarcinoma, benign urinary system neoplasm, breast disorder, breast neoplasm, bronchial neoplasm, bronchogenic carcinoma, carcinoma, central nervous system malformation, cervix disorder, colonic disorder, colorectal neoplasm, cutaneous neuroendocrine carcinoma, digestive system disorder, digestive system neoplasm, endocrine system disorder, epithelial neoplasm, esophageal disorder, female reproductive system disorder, female reproductive system neoplasm, gastric neoplasm, gonadal disorder, hepatocellular carcinoma, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, intestinal disorder, kidney cancer, kidney disorder, liver disorder, lung disorder, lung neoplasm, malignant endocrine neoplasm, melanocytic neoplasm, melanoma, nasopharyngeal carcinoma, nasopharyngeal disorder, nasopharyngeal neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuroendocrine carcinoma, neuroendocrine neoplasm, neuromuscular disease, non-small cell lung carcinoma, otorhinolaryngologic disease, ovarian cancer, ovarian disorder, peripheral nervous system disorder, polyneuropathy, polyomavirus infectious disease, primitive neuroectodermal tumor, rectal disorder, renal cell carcinoma, respiratory system disorder, respiratory tract neoplasm, skin disorder, skin neoplasm, small cell lung carcinoma, stomach disorder, transitional cell carcinoma, triple-negative breast carcinoma, urinary system disorder, uterine disorder, viral infectious disease | Recruiting | Phase 1 / Phase 2 | 2026-08-06 | NCT07749586 | |
| Pancreatic Cancer Registry: For Any Person With a Personal or Family History | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Neoplasms by Site, central nervous system malformation, endocrine system disorder, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, malignant endocrine neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, pancreas disorder, pancreatic neoplasm, peripheral nervous system disorder, polyneuropathy | Recruiting | Not stated | 2026-08-05 | NCT02886247 | |
| A Study of ART0380 for the Treatment of Advanced or Metastatic Solid Tumors | Adnexal Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Neoplasm Metastasis, Neoplasms by Histologic Type, Neoplasms by Site, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, Urogenital Neoplasms, acinar cell carcinoma, adenocarcinoma, carcinoma, central nervous system malformation, colonic disorder, colorectal neoplasm, digestive system disorder, digestive system neoplasm, endocrine system disorder, endometrium neoplasm, epithelial neoplasm, fallopian tube cancer, fallopian tube disorder, fallopian tube neoplasm, female reproductive system disorder, female reproductive system neoplasm, gonadal disorder, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, intestinal disorder, malignant endocrine neoplasm, metastatic malignant neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, ovarian cancer, ovarian disorder, pancreatic ductal adenocarcinoma, peripheral nervous system disorder, polyneuropathy, primary peritoneal carcinoma, rectal disorder, uterine disorder | Recruiting | Phase 1 / Phase 2 | 2026-07-30 | NCT04657068 | |
| Cryotherapy, PGE2, NGF Levels and Pain After Endodontic Retreatment | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurologic Manifestations, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Postoperative Pain, Signs and Symptoms, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Not yet recruiting | Not applicable | 2026-07-29 | NCT07733700 | |
| HPB-092 for the Treatment of Relapsed and Refractory Acute Myeloid Leukemia | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, acute myeloid leukemia, central nervous system malformation, hematologic disorder, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, leukemia, myeloid leukemia, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 1 | 2026-07-23 | NCT07137637 | |
| Online Study of People Who Have Genetic Changes and Features of Autism: Simons Searchlight | 2q37 microdeletion syndrome, Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cri-du-chat syndrome, Koolen-de Vries syndrome due to 17q21.31 microdeletion syndrome, Neurobehavioral Manifestations, Neurologic Manifestations, autism spectrum disorder due to AUTS2 deficiency, central nervous system malformation, chromosomal disorder, chromosome 15q13.3 microdeletion syndrome, chromosome 15q24 deletion syndrome, chromosome 1q21.1 deletion syndrome, chromosome 1q21.1 duplication syndrome, cornea plana 1, autosomal dominant, developmental and epileptic encephalopathy, 4, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, intellectual disability, intellectual disability, X-linked 1, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, proximal 16p11.2 microdeletion syndrome, rhabdoid tumor predisposition syndrome 2 | Recruiting | Not stated | 2026-07-23 | NCT01238250 | |
| A Study to Assess the Safety and Tolerability of AZD1390 Given With Radiation Therapy in Patients With Brain Cancer | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, astrocytoma (excluding glioblastoma), brain cancer, brain disorder, central nervous system cancer, central nervous system disorder, central nervous system malformation, epithelial neoplasm, glioblastoma, glioma, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuroepithelial neoplasm, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, primitive neuroectodermal tumor, tumor of meninges | Active, not recruiting | Phase 1 | 2026-07-17 | NCT03423628 | |
| First-in-Human Study of Tersolisib (STX-478) as Monotherapy and in Combination With Other Antineoplastic Agents in Participants With Advanced Solid Tumors | Adnexal Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Head and Neck Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, Skin and Connective Tissue Diseases, Urogenital Diseases, Urogenital Neoplasms, Uterine Cervical Neoplasms, breast cancer, breast disorder, breast neoplasm, carcinoma, central nervous system malformation, cervix disorder, endocrine system disorder, endometrium neoplasm, epithelial neoplasm, female reproductive system disorder, female reproductive system neoplasm, gonadal disorder, head and neck squamous cell carcinoma, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, malignant endocrine neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, ovarian cancer, ovarian disorder, peripheral nervous system disorder, polyneuropathy, skin disorder, squamous cell carcinoma, uterine disorder | Recruiting | Phase 1 / Phase 2 | 2026-07-07 | NCT05768139 | |
| Sapanisertib and Serabelisib (PIKTOR) in Various Combinations in Patients With HR+/HER2- Advanced/Metastatic Breast Cancer | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Site, Skin and Connective Tissue Diseases, breast disorder, breast neoplasm, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, skin disorder | Recruiting | Phase 1 / Phase 2 | 2026-07-02 | NCT07558733 | |
| Concurrent Training vs Soleus Push-Ups on Neurogenesis-Related Biomarkers in Diabetic Neuropathy Patients | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Diabetes Complications, Nutritional and Metabolic Diseases, central nervous system malformation, diabetes mellitus, diabetic neuropathy, endocrine system disorder, glucose metabolism disease, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, type 2 diabetes mellitus | Not yet recruiting | Not applicable | 2026-06-30 | NCT07675720 | |
| Phase 1/2 Study of ETX-636 in Participants With Advanced Solid Tumors | Adnexal Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Head and Neck Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, Skin and Connective Tissue Diseases, Urogenital Diseases, Urogenital Neoplasms, Uterine Cervical Neoplasms, breast disorder, breast neoplasm, carcinoma, central nervous system malformation, cervix disorder, endocrine system disorder, endometrium neoplasm, epithelial neoplasm, female reproductive system disorder, female reproductive system neoplasm, gonadal disorder, head and neck squamous cell carcinoma, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, malignant endocrine neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, ovarian cancer, ovarian disorder, peripheral nervous system disorder, polyneuropathy, skin disorder, squamous cell carcinoma, uterine disorder | Recruiting | Phase 1 / Phase 2 | 2026-06-23 | NCT06993844 | |
| A Study of Reduced-dose Radiation in People With Metastatic Tumors With a Genetic Change | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasm Metastasis, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, metastatic malignant neoplasm, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy | Recruiting | Phase 2 | 2026-05-11 | NCT05010031 | |
| 24VA022; VATCH Alpelisib for TIE2/PIK3CA Pathway VAs | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, vascular malformation | Active, not recruiting | Phase 2 | 2026-04-22 | NCT07543822 | |
| A Study to Evaluate the Safety and Tolerability of TOS-358 in Women With HR+ HER2- Breast Cancer | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Site, Skin and Connective Tissue Diseases, breast disorder, breast neoplasm, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, skin disorder | Recruiting | Phase 1 | 2026-04-22 | NCT05683418 | |
| Inavolisib for PIK3CA Mutated Advanced Endometrial Cancer: MITO END-4 | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Neoplasms by Site, Urogenital Diseases, Urogenital Neoplasms, central nervous system malformation, endometrium neoplasm, female reproductive system disorder, female reproductive system neoplasm, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, uterine disorder | Not yet recruiting | Phase 2 | 2026-04-13 | NCT07522697 | |
| Dexmedetomidine Sublingual Film for the Ambulatory Treatment of Hyperadrenergic Autonomic Crisis in Patients With Familial Dysautonomia | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Riley-Day syndrome, autonomic nervous system disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, primary dysautonomia | Enrolling by invitation | Phase 2 | 2026-04-13 | NCT06148311 | |
| 9-ING-41 in Patients With Advanced Cancers | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Leukemia-Lymphoma, Adult T-Cell, Male Urogenital Diseases, Neoplasm Metastasis, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Connective and Soft Tissue, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, T-cell leukemia, Thoracic Neoplasms, Urogenital Diseases, Urogenital Neoplasms, benign urinary system neoplasm, bone cancer, bone disorder, bone neoplasm, breast disorder, breast neoplasm, cancer, central nervous system malformation, colonic disorder, colorectal neoplasm, digestive system disorder, digestive system neoplasm, endocrine system disorder, epithelial neoplasm, glioma, hematologic disorder, hereditary disease, hereditary sensory and autonomic neuropathy, immune system disorder, immunoproliferative disorder, inherited neurodegenerative disorder, intestinal disorder, kidney cancer, kidney disorder, leukemia, lung disorder, lung neoplasm, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, malignant endocrine neoplasm, malignant glioma, malignant pancreatic neoplasm, musculoskeletal system disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuroepithelial neoplasm, neuromuscular disease, pancreas disorder, pancreatic adenocarcinoma, pancreatic neoplasm, peripheral nervous system disorder, polyneuropathy, primitive neuroectodermal tumor, rectal disorder, refractory malignant neoplasm, respiratory system disorder, respiratory tract neoplasm, sarcoma, skin disorder, urinary system disorder | Active, not recruiting | Phase 2 | 2026-04-03 | NCT03678883 |