neuromuscular disease caused by qualitative or quantitative defects of dystrophin
neuromuscular disease caused by qualitative or quantitative defects of dystrophin
Explore linked clinical trials. Standard reference: MONDO:00161473 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| VirtualPark_Pediatric | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, Thomsen and Becker disease, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular disease caused by qualitative or quantitative defects of dystrophin | Recruiting | Not applicable | 2026-08-11 | NCT07580365 | |
| Duchenne Electronic Health Record Study | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, neuromuscular disease caused by qualitative or quantitative defects of dystrophin | Recruiting | Not stated | 2026-05-27 | NCT07609394 | |
| The Duchenne Registry | Becker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, neuromuscular disease caused by qualitative or quantitative defects of dystrophin | Recruiting | Not stated | 2026-05-08 | NCT02069756 |