congenital dyserythropoietic anemia
congenital dyserythropoietic anemia
Explore linked clinical trials. Standard reference: MONDO:00194034 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| The Congenital Dyserythropoietic Anemia Registry (CDAR) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, congenital dyserythropoietic anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease | Recruiting | Not stated | 2026-06-16 | NCT02964494 | |
| Zoledronic Acid Treatment in Patients With Congenital Dyserythropoietic Anemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, congenital dyserythropoietic anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease | Recruiting | Phase 1 / Phase 2 | 2026-03-13 | NCT07471516 | |
| Integrative Diagnosis for SCD and Other RADs | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, anemia, congenital dyserythropoietic anemia, disease, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, hereditary spherocytosis, inherited hemoglobinopathy, sickle cell disease, thalassemia | Recruiting | Not stated | 2025-10-03 | NCT07206095 | |
| RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, alpha thalassemia spectrum, anemia, beta thalassemia, bone marrow disorder, congenital dyserythropoietic anemia, cystinosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary anemia, hereditary disease, inborn errors of metabolism, inherited aplastic anemia, inherited hemoglobinopathy, iron metabolism disease, lysosomal storage disease, metabolic disease, myelodysplastic syndrome, pyruvate kinase deficiency of red cells, sickle cell disease, sideroblastic anemia, thalassemia | Recruiting | Not stated | 2024-01-19 | NCT06213402 |