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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
The Congenital Dyserythropoietic Anemia Registry (CDAR)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, congenital dyserythropoietic anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary diseaseRecruitingNot stated2026-06-16NCT02964494
Zoledronic Acid Treatment in Patients With Congenital Dyserythropoietic AnemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, congenital dyserythropoietic anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary diseaseRecruitingPhase 1 / Phase 22026-03-13NCT07471516
Integrative Diagnosis for SCD and Other RADsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, anemia, congenital dyserythropoietic anemia, disease, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, hereditary spherocytosis, inherited hemoglobinopathy, sickle cell disease, thalassemiaRecruitingNot stated2025-10-03NCT07206095
RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, alpha thalassemia spectrum, anemia, beta thalassemia, bone marrow disorder, congenital dyserythropoietic anemia, cystinosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary anemia, hereditary disease, inborn errors of metabolism, inherited aplastic anemia, inherited hemoglobinopathy, iron metabolism disease, lysosomal storage disease, metabolic disease, myelodysplastic syndrome, pyruvate kinase deficiency of red cells, sickle cell disease, sideroblastic anemia, thalassemiaRecruitingNot stated2024-01-19NCT06213402