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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIMBlood Protein Disorders, DNA Virus Infections, Hemic and Lymphatic Diseases, Hypogammaglobulinemia, Infections, Skin Diseases, Viral, Skin and Connective Tissue Diseases, Tumor Virus Infections, agammaglobulinemia, common wart, hematologic disorder, human papilloma virus infection, immune system disorder, immunodeficiency disease, inborn error of immunity, lymphatic system disorder, lymphoproliferative syndrome, skin disorder, skin disorder caused by infection, viral infectious diseaseEnrolling by invitationPhase 1 / Phase 22026-10-09NCT07775313
Allogeneic Hematopoietic Stem Cell Transplant for GATA2 MutationsHemic and Lymphatic Diseases, anemia, bone marrow disorder, hematologic disorder, immune system disorder, immunodeficiency disease, inborn error of immunity, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasiaRecruitingPhase 22026-10-05NCT01861106
Genetic Analysis of Immune DisordersCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, immunodeficiency disease, inborn error of immunityRecruitingNot stated2026-09-25NCT00001467
Allogeneic Hematopoietic Stem Cell Transplantation With Briquilimab-Based Conditioning in Participants With GATA2 Deficiencyimmune system disorder, immunodeficiency disease, inborn error of immunityActive, not recruitingPhase 22026-08-11NCT05907746
Impact of a Strategy Based on Bacterial DNA Detection to Optimize Antibiotics in Immunocompromised Patients With Hospital-acquired Pneumonia Requiring Mechanical VentilationDisease Attributes, Healthcare-Associated Pneumonia, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Pneumonia, Ventilator-Associated, iatrogenic disease, immune system disorder, immunodeficiency disease, inborn error of immunity, lung disorder, nosocomial infection, pneumonia, respiratory system disorder, respiratory tract infectious disorderRecruitingNot applicable2026-08-07NCT05405491
A Phase II Study of Allogeneic Hematopoietic Stem Cell Transplant for Subjects With VEXAS (Vacuoles, E1 Enzyme, X-linked, Autoinflammatory, Somatic) SyndromeHemic and Lymphatic Diseases, autoimmune disease, bone marrow disorder, hematologic disorder, immune system disorder, immunodeficiency disease, inborn error of immunity, myelodysplastic syndromeRecruitingPhase 22026-07-10NCT05027945
Vaccine-induced Immunity in Immunocompromised Patientsimmune system disorder, immunodeficiency disease, inborn error of immunityRecruitingNot stated2026-05-12NCT06612515
Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCTBone Marrow Failure, Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, acquired aplastic anemia, anemia, bone marrow disorder, hematologic disorder, hemophagocytic syndrome, hereditary disease, immune system disorder, immunodeficiency disease, immunoproliferative disorder, inborn error of immunity, inborn errors of metabolism, inherited hemoglobinopathy, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, metabolic disease, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasia, neoplasmRecruitingPhase 1 / Phase 22026-04-15NCT06839456
OPtimisation of Antiviral Therapy in Immunocompromised COVID-19 Patients: a Randomized Factorial Controlled Strategy TrialCOVID-19, Coronaviridae Infections, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, immune system disorder, immunodeficiency disease, inborn error of immunity, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease, viral pneumoniaRecruitingPhase 22026-02-23NCT05587894
OPtimisation of Antiviral Therapy in Immunocompromised COVID-19 PatientsCOVID-19, Coronaviridae Infections, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, immune system disorder, immunodeficiency disease, inborn error of immunity, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease, viral pneumoniaRecruitingPhase 22026-02-18NCT07406217
Clozapine-related Immunodeficiency in Parkinsons DiseasePsychotic Disorders, Schizophrenia Spectrum and Other Psychotic Disorders, immune system disorder, immunodeficiency disease, inborn error of immunity, psychiatric disorderRecruitingPhase 42025-11-19NCT06634641
SYSTEMS-LEVEL ANALYSES OF IMMUNE DYSREGULATIONallergic disease, autoimmune disease, autoinflammatory syndrome, immune system disorder, immunodeficiency disease, inborn error of immunityRecruitingNot stated2024-02-08NCT06248957