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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann ThrombastheniaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingPhase 1 / Phase 22026-09-25NCT06211634
Videomicroscopy for the Prediction of Bleeding in Constitutional Haemorrhagic DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired)RecruitingNot applicable2026-05-20NCT04119908
ATHNdataset RegistryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism and Thrombosis, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, X-linked disease, anemia, arthropathy, blood coagulation disease, blood platelet disease, cardiovascular disorder, coagulation protein disease, familial hemolytic anemia, hemarthrosis, hematologic disorder, hemolytic anemia, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, inherited hemoglobinopathy, musculoskeletal system disorder, sickle cell disease, thrombotic disease, vascular disorder, vascular hemostatic disease, von Willebrand disease (hereditary or acquired)RecruitingNot stated2026-04-21NCT06820515
Eptacog Beta in Glanzmann's (HeT_LFB-Strength-Study_FID531)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 22025-12-01NCT07136857
The Genetics and Functional Basis of Inherited Platelet, White Blood Cell, Red Blood Cell, and Blood Clotting Disorders.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism and Thrombosis, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, cardiovascular disorder, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, thrombotic disease, vascular disorderRecruitingNot stated2025-10-20NCT00230165
Multinational Glanzmann StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderNot yet recruitingNot stated2024-02-28NCT06204042