15 results · Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Efficacy and Safety of Vamifeport in Adult Participants With Homeostatic Iron Regulator Gene (HFE)-Related Hereditary HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingPhase 22026-09-16NCT07332091
Fully Automated High-Throughput Quantitative MRI of the LiverDigestive System Diseases, Nutritional and Metabolic Diseases, fatty liver disease, iron metabolism disease, iron poisoning, liver disorder, metabolic diseaseRecruitingNot stated2026-09-16NCT05294471
Apotransferrin in AtransferrinemiaHemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, anemia, atransferrinemia, hematologic disorder, iron metabolism disease, iron poisoning, metabolic diseaseActive, not recruitingPhase 22026-09-16NCT01797055
Treatment of HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseActive, not recruitingPhase 22026-09-16NCT00007150
Early Screening and Treatment of Heart Complication in Sickle Cell DiseaseArrhythmias, Cardiac, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, anemia, cardiomyopathy, cardiovascular disorder, familial hemolytic anemia, heart disorder, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, iron metabolism disease, iron poisoning, metabolic disease, sickle cell diseaseRecruitingPhase 22026-09-09NCT07023666
Neurodegenerative Diseases Progression Markers (MARKERS-NDD)Alzheimer disease, Cognition Disorders, Cognitive Dysfunction, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Frontotemporal Lobar Degeneration, Lewy body dementia, Neurologic Manifestations, Nutritional and Metabolic Diseases, Ocular Motility Disorders, Parkinson disease, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, amyotrophic lateral sclerosis, autonomic nervous system disorder, basal ganglia disorder, brain disorder, central nervous system disorder, cognitive disorder, corticobasal degeneration disorder, cranial nerve neuropathy, dementia, eye disorder, hereditary disease, inherited neurodegenerative disorder, iron metabolism disease, iron poisoning, metabolic disease, motor neuron disorder, movement disorder, multiple system atrophy, nervous system disorder, neuroaxonal dystrophy, neurodegeneration with brain iron accumulation, neurodegenerative disease, neuromuscular disease, ophthalmoplegia, palsy, pantothenate kinase-associated neurodegeneration, parkinsonian disorder, primary dysautonomia, proteostasis deficiencies, psychiatric disorder, spinal cord disorder, synucleinopathy, tauopathyRecruitingNot stated2026-09-02NCT06596746
Impact of Transferrin Saturation Guided Maintenance Treatment on Quality of Life in HFE HaemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, hereditary hemochromatosis, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseActive, not recruitingNot applicable2026-06-12NCT04779593
A Study to Evaluate BBI-001 in Healthy Volunteers and in Patients With Hereditary HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, hereditary hemochromatosis, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingPhase 1 / Phase 22026-05-13NCT07371793
Impact of Iron Overload on the Incidence of Liver Complications in Long-Term Survivors (≥10 Years) of Allogeneic Hematopoietic Stem-Cell Transplantation.Digestive System Diseases, Fibrosis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cirrhosis of liver, graft versus host disease, hemosiderosis, immune system disorder, iron metabolism disease, iron poisoning, liver disorder, metabolic diseaseRecruitingNot stated2026-04-27NCT07028112
Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, iron metabolism disease, iron poisoning, metabolic disease, thalassemiaNot yet recruitingNot stated2026-01-20NCT07352878
Ethnic Differences in Iron Absorption (FeGenes)Anemia, Hypochromic, Hemic and Lymphatic Diseases, Iron Deficiencies, Nutritional and Metabolic Diseases, anemia, hematologic disorder, iron deficiency anemia, iron metabolism disease, iron poisoning, metabolic diseaseActive, not recruitingNot stated2025-08-06NCT04198545
Heme and Non-heme Iron Intakes, Gut Microbiota, and Influence on Host Iron AbsorptionAnemia, Hypochromic, Hemic and Lymphatic Diseases, Iron Deficiencies, Nutritional and Metabolic Diseases, anemia, hematologic disorder, iron deficiency anemia, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingNot stated2025-02-24NCT06146608
Leflunomide for Idiopathic Pulmonary Hemosiderosis in ChildrenHemosiderosis, Pulmonary, Nutritional and Metabolic Diseases, hemosiderosis, iron metabolism disease, iron poisoning, lung disorder, metabolic disease, respiratory system disorderRecruitingPhase 1 / Phase 22023-07-10NCT05937191
An Observational Study Evaluating Patients With Chronic Liver Diseases Associated With Hepatic SteatosisCholangitis, Sclerosing, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, Fibrosis, Hepatitis, Chronic, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, autoimmune disease, autoimmune hepatitis, bile duct disorder, biliary tract disorder, cholangitis, cholestasis, chronic pancreatitis, cirrhosis of liver, digestive system disorder, fatty liver disease, gastroenteritis, hepatitis, hereditary disease, immune system disorder, inborn errors of metabolism, inborn metal metabolism disorder, inflammatory bowel disease, intestinal disorder, intrahepatic cholestasis, iron metabolism disease, iron poisoning, liver disorder, metabolic disease, metabolic dysfunction-associated steatotic liver disease, pancreas disorder, pancreatitis, primary biliary cholangitisRecruitingNot stated2022-04-19NCT05335603
China Registry for Genetic / Metabolic Liver DiseasesBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, hereditary hyperbilirubinemia, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, iron metabolism disease, iron poisoning, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseRecruitingNot stated2017-04-27NCT03131427