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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Vosoritide for Selected Genetic Causes of Short StatureBone Diseases, Developmental, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Dwarfism, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, bone disorder, cardiovascular disorder, congenital heart disease, connective tissue disorder, endocrine system disorder, heart disorder, hereditary disease, hypochondroplasia, musculoskeletal system disorderActive, not recruitingPhase 22026-03-18NCT04219007