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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS ICongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis I, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosisRecruitingPhase 12026-07-17NCT05682144