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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety and Efficacy Study of NGGT002 in Adult Patients With PhenylketonuriaBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 1 / Phase 22026-08-13NCT06687733
Safety and Efficacy Study of NGGT001 in Bietti Crystalline Corneoretinal Dystrophy SubjectsBietti crystalline corneoretinal dystrophyActive, not recruitingPhase 1 / Phase 22026-08-12NCT06706427