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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pilot Study of TTI-0102 in CystinosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, cystinosis, hereditary disease, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nephropathic cystinosisNot yet recruitingPhase 22026-09-23NCT07837726
A Dose-ranging Study of TTI-0102 in Adults and Children With Leigh Syndrome Spectrum (LSS)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Leigh syndrome, Nutritional and Metabolic Diseases, Pyruvate Metabolism, Inborn Errors, brain disorder, central nervous system disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, metabolic disease, nervous system disorderNot yet recruitingPhase 22026-07-24NCT06990984