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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderRecruitingPhase 1 / Phase 22026-04-15NCT07439887
Development and Evaluation of Functional Visual Field and Navigation Endpoints in Moderate to Profound Inherited Retinal Disease (DEFINE-IRD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt disease, eye disorder, hereditary disease, inherited retinal dystrophy, macular degeneration, retinal degeneration, retinal disorder, retinitis pigmentosa, retinoschisisRecruitingNot stated2026-03-31NCT07502664
Study to Evaluate Safety of RTx-015 Injection in Retinitis Pigmentosa or Choroideremia Patients (ENVISION)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, X-linked disease, choroideremia, eye disorder, hereditary disease, inherited retinal dystrophy, optic choroid disorder, retinal degeneration, retinal disorder, retinitis pigmentosa, uveal disorderActive, not recruitingPhase 12026-02-20NCT06460844
Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal DegenerationCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt disease, X-linked disease, choroideremia, eye disorder, hereditary disease, inherited retinal dystrophy, macular degeneration, optic choroid disorder, retinal degeneration, retinal disorder, retinitis pigmentosa, uveal disorderRecruitingNot stated2025-01-08NCT06375239