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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
GCB-001 in Treatment of Patients With Type II (SMA) Spinal Muscular AtrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Atrophy, Spinal, Type II, Spinal Muscular Atrophies of Childhood, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyEnrolling by invitationNot applicable2026-09-11NCT06772402
Ph+ ALL in Chinese Children: Diagnosis, Treatment, and SurvivalHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingNot stated2026-09-10NCT07813208
Venetoclax-Enhanced BUCY vs. Standard BUCY Conditioning in High-Risk AML and MDS Patients Undergoing Allo-HSCT (Ven-BUCY Study)Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, acute myeloid leukemia, bone marrow disorder, hematologic disorder, leukemia, myelodysplastic syndrome, myeloid leukemia, neoplasmRecruitingNot applicable2026-09-02NCT07183878
Blinatumomab Intensification for MRD-Negative Acute B-Cell Lymphoblastic Leukemia Before Allogeneic Hematopoietic Stem Cell TransplantationHemic and Lymphatic Diseases, Neoplasm, Residual, Neoplasms by Histologic Type, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingNot applicable2026-09-02NCT07003737
Safety and Efficacy of Iptacopan in Patients With High-Risk Transplantation-Associated Thrombotic MicroangiopathyCytopenia, Hemic and Lymphatic Diseases, blood platelet disease, hematologic disorder, thrombocytopenia, thrombotic microangiopathyRecruitingNot applicable2026-08-26NCT07347990
Ruxolitinib Plus Etanercept vs Ruxolitinib for Steroid-Refractory Severe Acute GVHDgraft versus host disease, immune system disorderRecruitingNot applicable2026-07-07NCT07184853
The Efficacy and Safety of Dapagliflozin in the Treatment of Hereditary Kidney Disease With Proteinuria in ChildrenFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urination Disorders, Urogenital Diseases, Urological Manifestations, proteinuria, urinary system disorderRecruitingPhase 32026-07-06NCT06890143
RD06-05 Universal CD19/BCMA CAR-T for Refractory Pediatric Autoimmune DiseasesFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, IgA glomerulonephritis, Male Urogenital Diseases, Multi-Drug Resistant Nephrotic Syndrome, Skin and Connective Tissue Diseases, Urogenital Diseases, autoimmune disease, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, nephritis, nephrosis, nephrotic syndrome, systemic lupus erythematosus, urinary system disorderNot yet recruitingEarly phase 12026-06-29NCT07674147
Symptom Cluster Heterogeneity and Gut Microbiota Mechanisms in Childhood Cancer SurvivorsHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Pathologic Processes, Pathological Conditions, Signs and Symptoms, acute myeloid leukemia, cancer, disease, epithelial neoplasm, glioma, hematologic disorder, leukemia, myeloid leukemia, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumor, syndromic diseaseRecruitingNot stated2026-06-05NCT07450872
Study on Influencing Factors of Skin Complications Related to Insulin Injection in Children With Type 1 Diabetes MellitusCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, skin disorderNot yet recruitingNot stated2026-05-29NCT07615803
Efficacy and Safety of Ruxolitinib Cream in Chinese Children Aged 2-11 Years With Non-segmental VitiligoSkin and Connective Tissue Diseases, hypopigmentation of the skin, skin disorder, skin pigmentation disorder, vitiligoNot yet recruitingPhase 32026-05-19NCT07595939
Exergame-Based Physical Activity Promotion for Children and Adolescents With Congenital Heart DiseaseCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderNot yet recruitingNot applicable2026-05-18NCT07593118
Effect of Vitamin A Supplementation on Idiopathic ScoliosisNutritional and Metabolic Diseases, idiopathic scoliosis, nutritional deficiency disease, nutritional disorder, vitamin A deficiency, vitamin deficiency disorderRecruitingNot applicable2026-05-15NCT07335991
Effect of Adenotonsillectomy on Spinal Curve Magnitude in Children With Sleep-Disordered BreathingApnea, Dyssomnias, Respiration Disorders, Sleep Disorders, Intrinsic, idiopathic scoliosis, nervous system disorder, obstructive sleep apnea syndrome, respiratory system disorder, sleep apnea syndrome, sleep-wake disorderRecruitingNot applicable2026-05-15NCT07332780
CD19/BCMA UCAR-T for B Cell-Related Autoimmune DiseaseFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, IgA glomerulonephritis, Male Urogenital Diseases, Multi-Drug Resistant Nephrotic Syndrome, Skin and Connective Tissue Diseases, Urogenital Diseases, autoimmune disease, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, nephritis, nephrosis, nephrotic syndrome, skin disorder, systemic sclerosis, urinary system disorderRecruitingEarly phase 12026-05-14NCT07586267
Adaptive Digital Exercise Rehabilitation for Children After CHD SurgeryCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderNot yet recruitingNot applicable2026-05-08NCT07574463
A Bio-Psycho-Social Medical Model-Based Study on Adolescent Female HPV Vaccination Behavior and Comprehensive InterventionBiopsychosocial Model; HPV; Vaccination HesitancyNot yet recruitingNot applicable2026-05-01NCT07562984
Application Construction and Effect Evaluation of Family-empowered Pulmonary Rehabilitation in School-age Children With AsthmaAsthma ChildhoodNot yet recruitingNot applicable2026-04-30NCT07558954
Construction and Validation of an Intelligent Ultrasound Diagnostic System for the Spectrum of Neuroblastoma in ChildrenNeuroblastic TumorsActive, not recruitingNot stated2026-04-24NCT07549425
Clinical Trial on Safety and Efficacy of Thoracoabdominal Endoscopic Surgical System for Pediatric SurgeryCholedochal Cyst Resection; Congenital or Acquired Surgical Conditions Requiring Minimally Invasive Surgery in Children; Fundoplication; Indications for Laparoscopic Thoracic and Abdominal Surgery in Children; Ovarian Tumor Resection; Pulmonary Segmentectomy; Pyeloplasty; Radical Operation for Hirschsprung Disease; Ureteral ReimplantationNot yet recruitingNot applicable2026-04-15NCT07530133
Safety and Efficacy of the AbsnowTM II Absorbable Atrial Septal Defect Closure System for Atrial Septal Defect Closure TherapyCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, atrial septal defect, cardiovascular disorder, congenital heart disease, heart disorder, heart septal defectNot yet recruitingNot applicable2026-04-14NCT07529028
Allogeneic CD19/BCMA CAR-T for B Cell-Related Autoimmune DiseaseFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, IgA glomerulonephritis, Male Urogenital Diseases, Multi-Drug Resistant Nephrotic Syndrome, Skin and Connective Tissue Diseases, Urogenital Diseases, anti-neutrophil cytoplasmic antibody-associated vasculitis, autoimmune disease, cardiovascular disorder, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, necrotizing vasculitis, nephritis, nephrosis, nephrotic syndrome, skin disorder, skin vascular disease, systemic sclerosis, urinary system disorder, vascular disorder, vasculitisRecruitingEarly phase 12026-04-02NCT07507201
Perioperative Lidocaine for Lung Protection in Infants Undergoing Cardiac SurgeryCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lung Injury, Thoracic Injuries, acute lung injury, cardiovascular disorder, congenital heart disease, heart disorder, injury, lung disorder, respiratory system disorderNot yet recruitingPhase 42026-03-30NCT07499154
Serum Copeptin as Biomarker for Diagnosis and Classification of Polyuric Primary Monosymptomatic Nocturnal EnuresisFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, diabetes insipidus, endocrine system disorder, kidney disorder, pituitary gland disorder, urinary system disorderNot yet recruitingNot stated2026-03-27NCT07496541
Exploratory Clinical Study on the Safety and Efficacy of Anti- CD19/BCMA CAR-NK Cell Injection for the Treatment of Refractory Pediatric Rheumatic DiseasesSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, musculoskeletal system disorder, rheumatic disorder, systemic lupus erythematosusRecruitingEarly phase 12026-03-24NCT07490041