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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Physical Activity in CKDChronic Disease, Chronic Kidney Diseases, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderRecruitingNot applicable2026-10-08NCT06624358
Validation of Nanosensor Oxygen MeasurementNutritional and Metabolic Diseases, inborn mitochondrial metabolism disorder, inborn mitochondrial myopathy, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 12026-10-07NCT06819683
Efficacy of Mirdametinib Alone or Combination With Radiotherapy for Germline and Sporadic NF1-Altered High-Grade GliomaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, astrocytoma (excluding glioblastoma), epithelial neoplasm, glioblastoma, glioma, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, neoplasm, nerve sheath neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neuroepithelial neoplasm, neurofibroma, neurofibromatosis, neurofibromatosis type 1, neuromuscular disease, peripheral nervous system disorder, primitive neuroectodermal tumorNot yet recruitingPhase 22026-10-05NCT07521657
Study of Cabozantinib With Selumetinib for Plexiform NeurofibromasCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Histologic Type, Neoplasms, Nerve Tissue, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, neoplasm, nerve sheath neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neurofibroma, neurofibromatosis, neurofibromatosis type 1, neuromuscular disease, peripheral nervous system disorder, peripheral nervous system neoplasm, plexiform neurofibromaRecruitingPhase 12026-10-02NCT06502171
Boosting Resources for Tracheostomy Care at HomeCaregiver Burden; TracheostomyEnrolling by invitationNot applicable2026-09-30NCT06283953
Down Syndrome Obstructive Sleep ApneaAbnormalities, Multiple, Apnea, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Down syndrome, Dyssomnias, Neurobehavioral Manifestations, Neurologic Manifestations, Respiration Disorders, Sleep Disorders, Intrinsic, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, obstructive sleep apnea syndrome, respiratory system disorder, sleep apnea syndrome, sleep-wake disorderRecruitingPhase 22026-09-30NCT06043440
A Study of GlcNAc on Tear Production in NGLY1-CDDGcongenital disorder of deglycosylation 1Active, not recruitingPhase 22026-09-29NCT05402345
CD19-Directed Chimeric Antigen Receptor Autologous T Cells (CART19) for LupusFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Skin and Connective Tissue Diseases, Urogenital Diseases, autoimmune disease, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, lupus nephritis, nephritis, systemic lupus erythematosus, urinary system disorderRecruitingPhase 1 / Phase 22026-09-24NCT06839976
Vancomycin Reduction Practices (VRP) in the NICUCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Systemic Inflammatory Response Syndrome, neonatal sepsisRecruitingNot applicable2026-09-24NCT06772675
Evaluating the Relationship Between Skin Color and Pulse Oximeter Accuracy in ChildrenHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, childhood acute lymphoblastic leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingNot stated2026-09-24NCT06529575
ALS20-101 Lentiviral Gene Therapy for Beta ThalassemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemiaRecruitingPhase 1 / Phase 22026-09-23NCT06364774
Evaluation of 18F-Fluciclovine Positron Emission Tomography - Magnetic Resonance Imaging (PET-MRI) in LGGNeoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, epithelial neoplasm, glioma, low grade glioma, malignant glioma, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumorRecruitingEarly phase 12026-09-22NCT05555550
Molecular Basis of Food AllergyDigestive System Diseases, Eosinophilia, Hemic and Lymphatic Diseases, Hypersensitivity, Immediate, digestive system disorder, eosinophilic esophagitis, esophageal disorder, esophagitis, food allergy, gastroenteritis, hematologic disorder, immune system disorder, leukocyte disorderEnrolling by invitationNot stated2026-09-21NCT01832324
SMART Implementation-Effectiveness Trial 2Asthma in ChildrenRecruitingNot applicable2026-09-18NCT07138027
SMART Implementation-Effectiveness Trial 1Asthma in ChildrenRecruitingNot applicable2026-09-18NCT07137923
Natural History Study of Mitochondrial MyopathyFatigue, Muscle Weakness, Neurologic Manifestations, Neuromuscular Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, inborn mitochondrial metabolism disorder, inborn mitochondrial myopathy, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-09-17NCT05250375
CEUS Evaluation of Hydrocephalus in Neonates and InfantsHydrocephalus Acquired; Hydrocephalus in InfantsRecruitingPhase 22026-09-16NCT06693752
Genetics of Insulin and Incretins in Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-09-16NCT01852448
Treating Young Children With Attention Deficit Hyperactivity Disorderattention deficit hyperactivity disorder, inattentive type, neurodevelopmental disorder, oppositional defiant disorder, psychiatric disorderRecruitingPhase 42026-09-14NCT07300956
Malabsorption Blood Test (MBT) to Determine Exocrine Pancreatic Function and Related Quality of Life in Chronic PancreatitisChronic Disease, Digestive System Diseases, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, chronic pancreatitis, exocrine pancreatic insufficiency, pancreas disorder, pancreatitis, recurrent acute pancreatitisRecruitingPhase 42026-09-11NCT07418593
I-DECIDE After Bronchiolitis HospitalizationBronchiolitis AcuteRecruitingNot applicable2026-09-10NCT07243652
A Study to Compare the Long-term Outcomes After Two Different AnaestheticsChemically-Induced Disorders, nervous system disorder, poisoning, toxic encephalopathyActive, not recruitingPhase 32026-09-10NCT03089905
Pilot Study of a Modified Safety Planning Intervention for Elementary School-Aged Children - Main StudySuicidal Behaviors; Suicidal IdeationEnrolling by invitationNot applicable2026-09-09NCT07564583
Li-Fraumeni Syndrome/TP53 BiobankCongenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Li-Fraumeni syndrome, Li-fraumeni-like syndrome, Nutritional and Metabolic Diseases, hereditary disease, hereditary neoplastic syndrome, metabolic disease, neoplasmRecruitingNot stated2026-09-04NCT04367246
Observational Approach Versus Surgical Intervention for StonesCalculi, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Kidney Calculi, Male Urogenital Diseases, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Urinary Calculi, Urogenital Diseases, kidney disorder, nephrolithiasis, urinary system disorder, urolithiasisRecruitingNot applicable2026-09-03NCT07718802