Swedish Orphan Biovitrum
Swedish Orphan Biovitrum
Explore linked clinical trials.21 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Emapalumab Prevention of CAR-T Cell Associated Toxicities | B-cell neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, diffuse large B-cell lymphoma, follicular lymphoma, high grade B-cell lymphoma, immune system disorder, immunoproliferative disorder, large B-cell lymphoma, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, primary mediastinal large B-cell lymphoma | Recruiting | Phase 2 | 2026-10-06 | NCT06550141 | |
| Pacritinib For Bone Marrow Fibrosis In Patients With Myelofibrosis Who Have Thrombocytopenia | Hemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosis | Recruiting | Phase 2 | 2026-10-02 | NCT07394153 | |
| Long-term Study Evaluating Joint Health in People With Haemophilia A Receiving Real-world Prophylactic Treatment With Efanesoctocog Alfa | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder | Active, not recruiting | Phase 4 | 2026-09-30 | NCT06940830 | |
| A Study to Assess the Effectiveness and Safety of Pacritinib in Patients With VEXAS Syndrome (PAXIS) | Hemic and Lymphatic Diseases, Neoplasms by Site, VEXAS syndrome, bone marrow disorder, hematologic disorder, hematopoietic and lymphoid system neoplasm, myelodysplastic syndrome, neoplasm | Active, not recruiting | Phase 2 | 2026-09-15 | NCT06782373 | |
| Pacritinib Effectiveness in Real-world Settings | Hemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosis | Recruiting | Not stated | 2026-09-14 | NCT07774455 | |
| Real-World Effectiveness and Safety of Pegcetacoplan in Patients With C3G or IC-MPG: A Multi-Country Study | Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Diseases, glomerulonephritis, kidney disorder, nephritis, urinary system disorder | Recruiting | Phase 4 | 2026-09-09 | NCT07746895 | |
| A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) | Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, anemia, bone marrow disorder, hematologic disorder, hemolytic anemia, myelodysplastic syndrome, paroxysmal nocturnal hemoglobinuria | Active, not recruiting | Not stated | 2026-09-03 | NCT05776472 | |
| A Study of Avatrombopag in Adults With Aplastic Anemia Who Did Not Respond to, Cannot Receive, or Had Return of Disease After Standard Treatment | Bone Marrow Failure Disorders, Disease Attributes, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, anemia, aplastic anemia, bone marrow disorder, disease, hematologic disorder | Not yet recruiting | Phase 2 / Phase 3 | 2026-08-26 | NCT07786922 | |
| Emapalumab MDA5 Rapidly Progressive Interstitial Lung Disease (RP-ILD) Study | Skin and Connective Tissue Diseases, amyopathic dermatomyositis, connective tissue disorder, dermatomyositis, interstitial lung disease, lung disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, polymyositis, respiratory system disorder, skin disorder | Recruiting | Phase 2 | 2026-08-25 | NCT07486869 | |
| Pacritinib With Standard of Care Azacitidine or Decitabine as a Bridge to Allogeneic Hematopoietic Stem Cell Transplant for Patients With Accelerated and Blast Phase Myeloproliferative Neoplasms | Accelerated Phase Myeloproliferative Neoplasm; Blast Phase Myeloproliferative Neoplasm | Recruiting | Phase 2 | 2026-08-19 | NCT07148947 | |
| Ultrasound Assessment of Joint Health in Patients With Mild Hemophilia (Factor Levels 5-40%) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, arthropathy, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, musculoskeletal system disorder | Not yet recruiting | Not applicable | 2026-08-17 | NCT07719647 | |
| Pacritinib in Vacuoles, E1 Ubiqutin-activating Enzyme, X-linked, Autoinflammatory, Somatic (VEXAS) Syndrome | VEXAS syndrome | Recruiting | Phase 1 | 2026-07-15 | NCT06538181 | |
| Study to Provide Continued Access to Treatment for Patients Completing a Previous Trial With Efanesoctocog Alfa | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, blood coagulation disease, coagulation protein disease, follicular lymphoma, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, immune system disorder, immunoproliferative disorder, inherited blood coagulation disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm | Recruiting | Phase 3 | 2026-06-26 | NCT06716814 | |
| A Study to Investigate the Course of Synovial Hypertrophy in Patients With Haemophilia A on Efanesoctocog Alfa Prophylaxis | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Synovial Hypertrophy, arthropathy, blood coagulation disease, coagulation protein disease, follicular lymphoma, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, immune system disorder, immunoproliferative disorder, inherited blood coagulation disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, musculoskeletal system disorder, neoplasm, synovitis | Active, not recruiting | Phase 4 | 2026-04-30 | NCT06752850 | |
| A Phase 3 Study of Pacritinib in Patients With Primary Myelofibrosis, Post Polycythemia Vera Myelofibrosis, or Post-Essential Thrombocythemia Myelofibrosis | Hemic and Lymphatic Diseases, Hypertrophy, Myeloproliferative Disorders, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Splenomegaly, anemia, blood platelet disease, bone marrow disorder, hematologic disorder, hemorrhagic disease, primary myelofibrosis | Active, not recruiting | Phase 3 | 2026-04-30 | NCT03165734 | |
| Effects of Anakinra in Subjects With Corticosteroid-resistant/Intolerant Meniere's Disease and Autoimmune Inner Ear Disease | Ear Diseases, Meniere disease, autoimmune inner ear disease, endolymphatic hydrops, inner ear disorder, otorhinolaryngologic disease | Recruiting | Phase 2 | 2026-04-15 | NCT03587701 | |
| Palifermin With Leuprolide Acetate for the Promotion of Immune Recovery Following Total Body Irradiation Based T-Cell Depleted Allogeneic Hematopoietic Stem Cell Transplantation | Blood Protein Disorders, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, bone marrow disorder, cardiovascular disorder, hematologic disorder, hemorrhagic disease, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, monoclonal gammopathy, myelodysplastic syndrome, neoplasm, non-Hodgkin lymphoma, plasma cell neoplasm, vascular disorder, vascular hemostatic disease | Active, not recruiting | Phase 2 | 2026-01-07 | NCT01746849 | |
| ITP Registry and Accompanying Biospecimen Collection | Cytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathy | Recruiting | Not stated | 2025-07-15 | NCT05152238 | |
| A Study of Anakinra in Japanese Patients With Still's Disease (SJIA and AOSD) | Juvenile-Onset Still Disease, Skin and Connective Tissue Diseases, adult-onset Still disease, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, juvenile idiopathic arthritis, musculoskeletal system disorder, rheumatic disorder, rheumatoid arthritis | Active, not recruiting | Phase 3 | 2025-03-05 | NCT05814159 | |
| Prevalence of Synovitis in Patients With Haemophilia A | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, arthropathy, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, musculoskeletal system disorder, synovitis | Recruiting | Not stated | 2024-04-16 | NCT06352216 | |
| A Trial Comparing the Efficacy and Safety of Anakinra Versus Intravenous Immunoglobulin (IVIG) Retreatment, in Patients With Kawasaki Disease Who Failed to Respond to Initial Standard IVIG Treatment | Hemic and Lymphatic Diseases, Kawasaki disease, Skin and Connective Tissue Diseases, cardiovascular disorder, lymphatic system disorder, skin disorder, skin vascular disease, vascular disorder, vasculitis | Recruiting | Phase 3 | 2024-02-28 | NCT04656184 |