21 results · Page 1 of 1

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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Emapalumab Prevention of CAR-T Cell Associated ToxicitiesB-cell neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, diffuse large B-cell lymphoma, follicular lymphoma, high grade B-cell lymphoma, immune system disorder, immunoproliferative disorder, large B-cell lymphoma, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, primary mediastinal large B-cell lymphomaRecruitingPhase 22026-10-06NCT06550141
Pacritinib For Bone Marrow Fibrosis In Patients With Myelofibrosis Who Have ThrombocytopeniaHemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosisRecruitingPhase 22026-10-02NCT07394153
Long-term Study Evaluating Joint Health in People With Haemophilia A Receiving Real-world Prophylactic Treatment With Efanesoctocog AlfaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingPhase 42026-09-30NCT06940830
A Study to Assess the Effectiveness and Safety of Pacritinib in Patients With VEXAS Syndrome (PAXIS)Hemic and Lymphatic Diseases, Neoplasms by Site, VEXAS syndrome, bone marrow disorder, hematologic disorder, hematopoietic and lymphoid system neoplasm, myelodysplastic syndrome, neoplasmActive, not recruitingPhase 22026-09-15NCT06782373
Pacritinib Effectiveness in Real-world SettingsHemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosisRecruitingNot stated2026-09-14NCT07774455
Real-World Effectiveness and Safety of Pegcetacoplan in Patients With C3G or IC-MPG: A Multi-Country StudyDisease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Diseases, glomerulonephritis, kidney disorder, nephritis, urinary system disorderRecruitingPhase 42026-09-09NCT07746895
A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, anemia, bone marrow disorder, hematologic disorder, hemolytic anemia, myelodysplastic syndrome, paroxysmal nocturnal hemoglobinuriaActive, not recruitingNot stated2026-09-03NCT05776472
A Study of Avatrombopag in Adults With Aplastic Anemia Who Did Not Respond to, Cannot Receive, or Had Return of Disease After Standard TreatmentBone Marrow Failure Disorders, Disease Attributes, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, anemia, aplastic anemia, bone marrow disorder, disease, hematologic disorderNot yet recruitingPhase 2 / Phase 32026-08-26NCT07786922
Emapalumab MDA5 Rapidly Progressive Interstitial Lung Disease (RP-ILD) StudySkin and Connective Tissue Diseases, amyopathic dermatomyositis, connective tissue disorder, dermatomyositis, interstitial lung disease, lung disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, nervous system disorder, neuromuscular disease, polymyositis, respiratory system disorder, skin disorderRecruitingPhase 22026-08-25NCT07486869
Pacritinib With Standard of Care Azacitidine or Decitabine as a Bridge to Allogeneic Hematopoietic Stem Cell Transplant for Patients With Accelerated and Blast Phase Myeloproliferative NeoplasmsAccelerated Phase Myeloproliferative Neoplasm; Blast Phase Myeloproliferative NeoplasmRecruitingPhase 22026-08-19NCT07148947
Ultrasound Assessment of Joint Health in Patients With Mild Hemophilia (Factor Levels 5-40%)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, arthropathy, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, musculoskeletal system disorderNot yet recruitingNot applicable2026-08-17NCT07719647
Pacritinib in Vacuoles, E1 Ubiqutin-activating Enzyme, X-linked, Autoinflammatory, Somatic (VEXAS) SyndromeVEXAS syndromeRecruitingPhase 12026-07-15NCT06538181
Study to Provide Continued Access to Treatment for Patients Completing a Previous Trial With Efanesoctocog AlfaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, blood coagulation disease, coagulation protein disease, follicular lymphoma, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, immune system disorder, immunoproliferative disorder, inherited blood coagulation disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasmRecruitingPhase 32026-06-26NCT06716814
A Study to Investigate the Course of Synovial Hypertrophy in Patients With Haemophilia A on Efanesoctocog Alfa ProphylaxisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Synovial Hypertrophy, arthropathy, blood coagulation disease, coagulation protein disease, follicular lymphoma, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, immune system disorder, immunoproliferative disorder, inherited blood coagulation disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, musculoskeletal system disorder, neoplasm, synovitisActive, not recruitingPhase 42026-04-30NCT06752850
A Phase 3 Study of Pacritinib in Patients With Primary Myelofibrosis, Post Polycythemia Vera Myelofibrosis, or Post-Essential Thrombocythemia MyelofibrosisHemic and Lymphatic Diseases, Hypertrophy, Myeloproliferative Disorders, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Splenomegaly, anemia, blood platelet disease, bone marrow disorder, hematologic disorder, hemorrhagic disease, primary myelofibrosisActive, not recruitingPhase 32026-04-30NCT03165734
Effects of Anakinra in Subjects With Corticosteroid-resistant/Intolerant Meniere's Disease and Autoimmune Inner Ear DiseaseEar Diseases, Meniere disease, autoimmune inner ear disease, endolymphatic hydrops, inner ear disorder, otorhinolaryngologic diseaseRecruitingPhase 22026-04-15NCT03587701
Palifermin With Leuprolide Acetate for the Promotion of Immune Recovery Following Total Body Irradiation Based T-Cell Depleted Allogeneic Hematopoietic Stem Cell TransplantationBlood Protein Disorders, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, bone marrow disorder, cardiovascular disorder, hematologic disorder, hemorrhagic disease, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, monoclonal gammopathy, myelodysplastic syndrome, neoplasm, non-Hodgkin lymphoma, plasma cell neoplasm, vascular disorder, vascular hemostatic diseaseActive, not recruitingPhase 22026-01-07NCT01746849
ITP Registry and Accompanying Biospecimen CollectionCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingNot stated2025-07-15NCT05152238
A Study of Anakinra in Japanese Patients With Still's Disease (SJIA and AOSD)Juvenile-Onset Still Disease, Skin and Connective Tissue Diseases, adult-onset Still disease, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, juvenile idiopathic arthritis, musculoskeletal system disorder, rheumatic disorder, rheumatoid arthritisActive, not recruitingPhase 32025-03-05NCT05814159
Prevalence of Synovitis in Patients With Haemophilia ACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, arthropathy, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, musculoskeletal system disorder, synovitisRecruitingNot stated2024-04-16NCT06352216
A Trial Comparing the Efficacy and Safety of Anakinra Versus Intravenous Immunoglobulin (IVIG) Retreatment, in Patients With Kawasaki Disease Who Failed to Respond to Initial Standard IVIG TreatmentHemic and Lymphatic Diseases, Kawasaki disease, Skin and Connective Tissue Diseases, cardiovascular disorder, lymphatic system disorder, skin disorder, skin vascular disease, vascular disorder, vasculitisRecruitingPhase 32024-02-28NCT04656184