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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
UCD19 CarT in Treatment of Pediatric B-ALL and B-NHLB-cell acute lymphoblastic leukemia, B-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Disease Attributes, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, Tumor Virus Infections, immune system disorder, immunoproliferative disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, viral infectious diseaseRecruitingPhase 1 / Phase 22026-09-14NCT04544592
Treatment of Obstructive Sleep Apnea With Personalized Surgery in Children With Down Syndrome (TOPS-DS)Abnormalities, Multiple, Apnea, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Down syndrome, Dyssomnias, Neurobehavioral Manifestations, Neurologic Manifestations, Respiration Disorders, Sleep Disorders, Intrinsic, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, obstructive sleep apnea syndrome, respiratory system disorder, sleep apnea syndrome, sleep-wake disorderRecruitingNot applicable2026-09-11NCT05508971
Immune Responses to GlutenDigestive System Diseases, Nutritional and Metabolic Diseases, celiac disease, digestive system disorder, intestinal disorder, malabsorption syndrome, metabolic diseaseEnrolling by invitationNot applicable2026-09-11NCT05209568
Sinus Disease in Young Children With Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Neurologic Manifestations, Olfactory Impairment, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, anosmia, cystic fibrosis, disease, hereditary disease, lung disorder, nervous system disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-09-10NCT06191640
Impact of Chemotherapy on Urinary Biomarkers and Non-Invasive Urodynamics in ChildrenBladder Dysfunction; Survivors of Childhood CancerRecruitingNot stated2026-09-09NCT04993859
Cabozantinib With Ifosfamide in Relapsed/Refractory SarcomasDisease Attributes, Ewing sarcoma, Neoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, connective tissue neoplasm, neoplasm, osteosarcoma, sarcomaRecruitingPhase 12026-09-03NCT06156410
Feasibility of a Modified Dental Comfort Position for Pediatric Patients Receiving Dental ExamsComfort; Dental Anxiety in Children; Feasibility StudiesNot yet recruitingNot applicable2026-09-01NCT07798141
De-implementing Inhaled Nitric Oxide for Congenital Diaphragmatic HerniaCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hernia, Hernia, Diaphragmatic, Internal Hernia, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, cardiovascular disorder, congenital diaphragmatic hernia, hypertensive disorder, lung disorder, pulmonary hypertension, respiratory system disorder, vascular disorderRecruitingPhase 42026-08-18NCT05213676
Feasibility of the Reality PAWS Program for Children in IsolationFeasibility Studies; Inpatient Pediatric Care; IsolationRecruitingNot applicable2026-08-14NCT07187245
Adapting a Psychosocial Support Intervention for the Rett Syndrome CommunityCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Rett syndrome, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorderNot yet recruitingNot applicable2026-07-28NCT07730112
Clinical and Basic Investigations Into Congenital Disorders of GlycosylationCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, congenital disorder of glycosylation, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, metabolic diseaseRecruitingNot stated2026-07-21NCT04199000
Parent Management Training to Treat IrritabilityAnger; Irritable Mood; Temper TantrumRecruitingNot applicable2026-07-15NCT06020261
Tendon-Bone Versus All-Soft-Tissue for ACL Reconstruction: A Patient-Blinded Randomized Clinical TrialAnterior Cruciate Ligament Injuries, Anterior Cruciate Ligament Tear, Knee Injuries, Leg Injuries, injuryActive, not recruitingNot applicable2026-07-13NCT04039971
The Treatment of Type I Open Fractures in PediatricsFractures, Open, bone fracture, injuryRecruitingNot applicable2026-07-01NCT00870064
Rett Syndrome RegistryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Rett Syndrome, Atypical, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorderRecruitingNot stated2026-06-30NCT05432349
Advanced SPinal Innovations With Robotics and Enabling Technology Registryadolescent idiopathic scoliosis, bone disorder, idiopathic scoliosis, musculoskeletal system disorder, spondylolisthesis, spondylolysis, spondylosis, vertebral column disorderRecruitingNot stated2026-06-22NCT05071144
Catheter-Related Early Thromboprophylaxis With Enoxaparin StudiesCritical Illness, Deep Vein Thrombosis, Disease Attributes, Embolism and Thrombosis, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Thromboembolism, Venous Thrombosis, cardiovascular disorder, thrombotic disease, vascular disorder, venous thromboembolismRecruitingPhase 2 / Phase 32026-06-08NCT04924322
Cerebral Palsy Adult Transition Longitudinal StudyBrain Damage, Chronic, Gait Disorders, Neurologic, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, cerebral palsy, nervous system disorderActive, not recruitingNot stated2026-06-08NCT02137005
Osteochondritis Dissecans of Knee Prospective CohortOsteochondritis, bone disorder, musculoskeletal system disorder, osteochondritis dissecansRecruitingNot stated2026-05-27NCT02771496
GLP-1 Agonist Therapy in Cystic Fibrosis-Related Glucose IntoleranceCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, cystic fibrosis, diabetes mellitus, endocrine system disorder, exocrine pancreatic insufficiency, glucose intolerance, glucose metabolism disease, hereditary disease, hyperglycemia, lung disorder, metabolic disease, pancreas disorder, respiratory system disorderRecruitingPhase 22026-05-18NCT04731272
Identification of Best Postoperative Analgesia Method Following a Minimally Invasive Repair of Pectus ExcavatumBone Diseases, Developmental, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Musculoskeletal Abnormalities, Neurologic Manifestations, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Postoperative Pain, Signs and Symptoms, bone disorder, musculoskeletal system disorder, pectus excavatumActive, not recruitingNot applicable2026-04-28NCT04211935
Liver Disease in Urea Cycle DisordersBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Citrullinemia 1, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, X-linked disease, arginase deficiency, argininosuccinic aciduria, brain disorder, central nervous system disorder, citrullinemia, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, liver disorder, metabolic disease, nervous system disorder, ornithine carbamoyltransferase deficiency, urea cycle disorderActive, not recruitingNot stated2026-04-27NCT04612764
24VA021; VATCH Trametinib for Ras/MAPK Pathway VAsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, vascular malformationActive, not recruitingPhase 22026-04-24NCT07549646
ACTEMRA® for the Treatment of Pediatric Adamantinomatous CraniopharyngiomaNeoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, adamantinous craniopharyngioma, craniopharyngioma, neoplasm, primitive neuroectodermal tumorRecruitingPhase 22026-04-23NCT05233397
24VA022; VATCH Alpelisib for TIE2/PIK3CA Pathway VAsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, central nervous system malformation, hereditary disease, hereditary sensory and autonomic neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, vascular malformationActive, not recruitingPhase 22026-04-22NCT07543822