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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Neonatal Enhanced Recovery After Surgery (ERAS) Outcomes StudyCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and AbnormalitiesNot yet recruitingNot stated2026-10-01NCT07771478
Children's Intensive Care Outcomes and Health Inequities: A Mixed Methods Study of Social Determinants in Paediatric Intensive Care in EnglandPaediatric Intensive CareNot yet recruitingNot stated2026-08-18NCT07771179
Pediatric Expansion Study of the Sentio SystemEar Diseases, Hearing Loss, Conductive, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, hearing disorder, hearing loss disorder, hearing loss, mixed conductive-sensorineural, nervous system disorder, otorhinolaryngologic diseaseActive, not recruitingNot applicable2026-08-14NCT06976086
Cerebellar Mutism Syndrome StudyNeoplasms by Site, Neurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system cancer, central nervous system disorder, communication disorder, language disorder, mutism, neoplasm, nervous system disorder, neurodevelopmental disorder, psychiatric disorder, speech disorderRecruitingNot stated2026-08-12NCT02300766
Metagenomics for Ocular InflammationInfections, eye disorder, uveal disorder, uveitisRecruitingNot stated2026-07-21NCT06974162
Adalimumab Dose Adjustment for Pediatric Uveitis Treatment Trialanterior uveitis, eye disorder, intermediate uveitis, panuveitis, uveal disorder, uveitisNot yet recruitingPhase 42026-07-13NCT07699107
Multi-omics Study in Citrin DeficiencyAdult-onset citrullinemia type 2Active, not recruitingNot stated2026-06-02NCT06895746
The Children's Adaptive Deep Brain Stimulation for Epilepsy TrialCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Epileptic Syndromes, Lennox-Gastaut syndrome, brain disorder, central nervous system disorder, epilepsy, hereditary disease, nervous system disorderRecruitingNot applicable2026-04-07NCT06924086
Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IICongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, X-linked disease, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 2, nervous system disorderActive, not recruitingPhase 1 / Phase 22026-03-27NCT05665166
DTG/3TC Fixed Dose Formulations for the Maintenance of Virological Suppression in Children With HIV Infection Aged 2 to <15 Years OldBlood-Borne Infections, Genital Diseases, HIV infectious disease, Infections, RNA Virus Infections, Urogenital Diseases, immune system disorder, inborn error of immunity, infectious disease, lentivirus infection, sexually transmitted disease, uterine carcinosarcoma, viral infectious disease, viral sexually transmitted diseaseActive, not recruitingPhase 2 / Phase 32026-03-04NCT04337450
Advanced MRI in IVHIntraventricular Hemorrhage Neonatal; Post-hemorrhagic HydrocephalusNot yet recruitingNot applicable2026-02-17NCT07412886
Thalamic Recordings in Children Undergoing SEEGbrain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorderRecruitingNot applicable2026-02-02NCT06453759
Evaluation of Aid to Diagnosis for Congenital Dysplasia of the Hip in General PracticeCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hip Dislocation, Joint Dislocations, Musculoskeletal Abnormalities, arthropathy, developmental dysplasia of the hip, musculoskeletal system disorderActive, not recruitingNot applicable2026-01-15NCT04101903
Base Edited CAR T Cells Against AML: Deep Conditioning Ahead of Allogeneic Stem Cell TransplantationHemic and Lymphatic Diseases, Neoplasms by Histologic Type, acute myeloid leukemia, hematologic disorder, leukemia, myeloid leukemia, neoplasmActive, not recruitingPhase 12026-01-14NCT05942599
An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCIDCongenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunity, metabolic disease, severe combined immunodeficiency, severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiencyEnrolling by invitationNot stated2025-12-18NCT04049084
Boost Brittle Bones Before BirthBone Diseases, Developmental, Collagen Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia, osteogenesis imperfectaActive, not recruitingPhase 1 / Phase 22025-09-12NCT03706482
Muscle Connective Tissue in Limb Development and DiseaseRadial DysplasiaRecruitingNot stated2025-08-27NCT02611089
Repurposing Empagliflozin for DMD-associated Cardiomyopathy in Children 6-18 Years of Agedilated cardiomyopathy 3BNot yet recruitingPhase 22025-08-15NCT06643442
Calprotectin and Gut Disease StudyCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, cardiovascular disorder, congenital heart disease, digestive system disorder, enterocolitis, gastroenteritis, heart disorder, intestinal disorder, necrotizing enterocolitisNot yet recruitingNot stated2025-08-08NCT07112794
CCHS Secure Health-hub Advancing Research Efforts (CCHS SHARE)Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, central hypoventilation syndrome, congenital, 1, with or without Hirschsprung diseaseRecruitingNot stated2025-07-16NCT06554275
Primary Posterior Tracheopexy Prevents Tracheal CollapseCartilage Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, Musculoskeletal Abnormalities, Skin and Connective Tissue Diseases, Tracheobronchomalacia, congenital tracheomalacia, connective tissue disorder, digestive system disorder, esophageal atresia, esophageal atresia/tracheoesophageal fistula, esophageal disorder, musculoskeletal system disorder, respiratory system disorder, tracheal disorderEnrolling by invitationNot applicable2025-03-30NCT06335862
Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type IIIACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3AActive, not recruitingPhase 1 / Phase 22025-03-30NCT04201405
Gut Health in Children With CancerB-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasms by Histologic Type, Tumor Virus Infections, acute myeloid leukemia, hematologic disorder, hemophagocytic syndrome, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, myeloid leukemia, neoplasm, viral infectious diseaseRecruitingNot stated2025-03-28NCT06899581
Inherited Cardiac cONditions In Kidscardiovascular disorderRecruitingNot stated2025-03-05NCT05158738
The Prevalence of RYR1-related DiseaseBody Temperature Changes, Congenital Fiber Type Disproportion, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hyperthermia, Intraoperative Complications, Minicore Myopathy with External Ophthalmoplegia, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Signs and Symptoms, Thomsen and Becker disease, central core myopathy, centronuclear myopathy, congenital myopathy, congenital structural myopathy, hereditary disease, inherited neurodegenerative disorder, malignant hyperthermia of anesthesia, muscle tissue disorder, musculoskeletal system disorder, myotonic syndrome, nemaline myopathy, nervous system disorder, neurodegenerative disease, neuromuscular diseaseNot yet recruitingNot stated2025-01-24NCT06791369