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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ichthyosiform Erythroderma, Congenital, Infant, Newborn, Diseases, Netherton syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, hereditary disease, hereditary skin disorder, ichthyosis, keratosis, skin disorderRecruitingPhase 12026-08-27NCT06539507
Berotralstat Treatment in Children With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 32026-02-25NCT05453968
Open-label Berotralstat Access to HAE Patients Previously Enrolled in Berotralstat StudiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderEnrolling by invitationPhase 32025-12-23NCT04933721