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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann ThrombastheniaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Glanzmann thrombasthenia 1, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderActive, not recruitingPhase 1 / Phase 22026-09-25NCT06211634
A First-in-Human Study to Assess the Safety, Pharmacokinetics, and Pharmacodynamics of HMB-003 in Healthy VolunteersHealthy Adult ParticipantsRecruitingPhase 12026-09-10NCT07798505
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic DisordersCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism and Thrombosis, Hemic and Lymphatic Diseases, Skin and Connective Tissue Diseases, X-linked disease, anemia, blood coagulation disease, blood platelet disease, cardiovascular disorder, coagulation protein disease, connective tissue disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, inherited hemoglobinopathy, sickle cell disease, thalassemia, thrombophilia, thrombotic disease, vascular disorder, vascular hemostatic disease, von Willebrand disease (hereditary or acquired)RecruitingNot stated2026-08-17NCT04398628
A Clinical Study to Assess Sutacimig in Participants With Congenital Factor VII DeficiencyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, congenital factor VII deficiency, factor VII deficiency, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 22026-07-22NCT07347249
A Study Assessing HMB-002 in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 3RecruitingPhase 1 / Phase 22026-06-30NCT06754852
A Study of Bleeding and Treatment in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 2, von Willebrand disease 3, von Willebrand disease type 2A, von Willebrand disease type 2M, von Willebrand disease type 2NRecruitingNot stated2026-04-21NCT06610201