National Organization for Rare Disorders
National Organization for Rare Disorders
Explore linked clinical trials.4 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| The Appendix Cancer PMP Research Foundation Natural History Study/Patient Registry | Abdominal Neoplasms, Digestive System Diseases, Digestive System Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, Peritoneal Diseases, adenocarcinoma, appendiceal neoplasm, carcinoma, cecal disorder, cecal neoplasm, cystic, mucinous, and serous neoplasm, digestive system disorder, digestive system neoplasm, epithelial neoplasm, intestinal disorder, mucinous adenocarcinoma, neoplasm, peritoneal neoplasm, pseudomyxoma peritonei | Recruiting | Not stated | 2026-08-17 | NCT07769346 | |
| Modulating Cerebellar Activity With Low-intensity Focused Ultrasound Stimulation for Primary Orthostatic Tremor | Orthostatic Tremor | Active, not recruiting | Not applicable | 2026-02-24 | NCT05547620 | |
| Global PNH Patient Registry | Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, anemia, bone marrow disorder, hematologic disorder, hemolytic anemia, myelodysplastic syndrome, paroxysmal nocturnal hemoglobinuria | Recruiting | Not stated | 2025-02-20 | NCT05755867 | |
| MyVHL: Patient Natural History Study | Abnormalities, Multiple, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, angiomatosis, cardiovascular disorder, hereditary disease, hereditary leiomyomatosis and renal cell cancer, hereditary neoplastic syndrome, neoplasm, nervous system disorder, neurocutaneous syndrome, vascular disorder, von Hippel-Lindau disease | Recruiting | Not stated | 2024-04-26 | NCT03749980 |